- “Overlap Syndrome and PSC: Evaluating Role of Gut Microflora and Its Identification With Antibiotics in Children”
- A Pilot Study Examining Diet in Primary Sclerosing Cholangitis
- A Pilot Study of Vancomycin or Metronidazole in Patients With Primary Sclerosing Cholangitis
- A Pilot Study of Xifaxan to Treat Patients With PSC
- A Pilot Study to Characterize Bile Acid Metabolism and Dysbiosis in Primary Sclerosing Cholangitis
- A POC and Dose-Ranging Study of HTD1801 in PSC Patients
- A Research Study to Evaluate Safety and Efficacy of DUR-928 in Subjects With Primary Sclerosing Cholangitis (PSC)
- A Single-arm,Phase IIa,Safety and Efficacy Trial of Selected MSCs in the Treatment of Patients With PSC & AiH
- A Study Evaluating the Safety and Efficacy of Curcumin in Patients With Primary Sclerosing Cholangitis (PSC)
- A Study of HTD1801 in Adolescents With Primary Sclerosing Cholangitis (PSC)
- A Study of HTD1801 in Healthy Subjects
- A Study of Oral Hymecromone to Treat Adults With Primary Sclerosing Cholangitis
- A Study Of Ursolic Acid For Primary Sclerosing Cholangitis
- A Study to Evaluate Efficacy and Safety of an Investigational Drug Named Volixibat in Patients With Itching Caused by Primary Sclerosing Cholangitis
- A Study to Evaluate the Safety, and Tolerability, and Efficacy of Seladelpar in Patients With PSC
- A Systems Biology Approach for Identification of Host and Microbial Mechanisms and Druggable Targets for the Treatment of PSC-IBD
- A Trial of BTT1023 in Patients With Primary Sclerosing Cholangitis
- A-LiNK: Improving Outcomes in Autoimmune Liver Disease
- An Efficacy Trial of Low Dose All-trans Retinoic Acid in Patients With Primary Sclerosing Cholangitis
- Biliary Excretion of Conjugated Bile Acids in Humans Measured by 11C-cholylsarcosine PET/CT
- Biliary Interventions in Critically Ill Patients With Secondary Sclerosing Cholangitis (BISCIT)
- Biobank for Cholestatic Liver Diseases.
- Characterization of Biliary Cell-derived Organoids From Bile of PSC and Non-PSC Patients
- Cholangioscopy in Primary Sclerosing Cholangitis (PSC)
- Cholangioscopy Using Narrow Band Imaging (NBI) in Patients With Primary Sclerosing Cholangitis (PSC) Undergoing Endoscopic Retrograde Cholangiopancreatogram (ERCP)
- Clinical Application of Annual Liver Multiscan and MRCP+ in Primary Sclerosing Cholangitis
- Clinical Utility of the Spyglass System in Primary Sclerosing Cholangitis (PSC)
- CM-101 in PSC Patients -The SPRING Study
- Combination Therapy With Ursodeoxycholic Acid (UDCA) and All-Trans Retinoic Acid (ATRA) for Treatment of Primary Sclerosing Cholangitis
- Compare Conventional Colonosocpy to Endoscopic AFI, NBI for Dysplasia Detection for Ulcerative Colitis & Cholangitis
- Detection of Advanced Colorectal Neoplasia by Stool DNA in Inflammatory Bowel Disease
- Development of a Patient-Reported Outcome Measure to Assess Symptoms in Patients With Primary Sclerosing Cholangitis (PSC)
- Disease Status in Primary Sclerosing Cholangitis by Elastography
- Effect and Safety of Oral Vancomycin in Primary Sclerosing Cholangitis Patients
- Effect of Simvastatin on the Prognosis of Primary Primary Sclerosing Cholangitis (PSC)
- Efficacy and Safety of Vedolizumab Intravenous (IV) in the Treatment of Primary Sclerosing Cholangitis in Subjects With Underlying Inflammatory Bowel Disease
- Efficacy of 24 Month of Bezafibrate in Primary Sclerosing Cholangitis With Persistent Cholestasis Despite Ursodeoxycholic Acid Therapy
- Endomicroscopy in Primary Sclerosing Cholangitis Related Inflammatory Bowel Disease Surveillance
- Endoscopic Ultrasound as an Early Diagnostic Tool for Primary Sclerosing Cholangitis
- Erlotinib for Chemoprevention in Trisomy 7 Positive Primary Sclerosing Cholangitis (PSC)
- Evaluation of DHA for the Treatment of PSC
- Fecal Microbiota Transplantation for the Treatment of Primary Sclerosing Cholangitis.
- Gastrointestinal Microbiota in Primary Sclerosing Cholangitis and Biliary Atresia With Vancomycin
- Genomics of Primary Sclerosing Cholangitis (PSC)
- Liver Transplantation for Hilar Cholangiocarcinoma in Association With Neoadjuvant Radio- and Chemo-therapy
- Minocycline in Primary Sclerosing Cholangitis (PSC)
- Mitomycin C Therapy for Patients With Primary Sclerosing Cholangitis
- MRI Based Biomarkers in Pediatric Autoimmune Liver Disease
- MRI Biomarkers in as Predictor of Clinical Endpoints in Pediatric Autoimmune Liver Disease
- Multicenter Observational Study of PSC and IgG4-SC in China
- National Database on Primary Sclerosing Cholangitis (PSC)
- NKT Role in the Regulation of the Inflammatory Bowel Disease
- Norursodeoxycholic Acid in the Treatment of Primary Sclerosing Cholangitis
- norUrsodeoxycholic Acid vs Placebo in PSC
- NPD Measurements in PSC Patients
- NPDT Evaluation in Children With CFTR and (PSC)
- Obeticholic Acid (OCA) in Primary Sclerosing Cholangitis (PSC)
- Open Label Study to Evaluate Safety and Efficacy of LUM001 in Patients With Primary Sclerosing Cholangitis
- Oral Hymecromone to Treat Adolescents and Adults With Primary Sclerosing Cholangitis.
- Paternally Inherited Phenotypes in Cholestasis
- PERSEUS: Preliminary Efficacy and Safety of Cenicriviroc in Adult Participants With Primary Sclerosing Cholangitis
- Pharmacokinetics and Pharmacodynamics of Cilofexor in Adults With Normal and Impaired Hepatic Function
- Phase 2 Study of NGM282 in Patients With Primary Sclerosing Cholangitis
- Phase 2a Evaluation of Safety, Tolerability, and Pharmacokinetics of PLN-74809 in Patients With Primary Sclerosing Cholangitis (PSC)
- Phase II Pilot Study of Cladribine (2-Chlorodeoxyadenosine; 2-CdA) for Early Stage Primary Sclerosing Cholangitis
- Pilot Study of Budesonide for Patients With Primary Sclerosing Cholangitis
- Pilot Study of Fenofibrate for PSC
- Predictive Models of Hepatic Decompensation and Survival Outcomes in Pediatric Patients With Cirrhosis
- Primary Sclerosing Cholangitis in Children
- Primary Sclerosing Cholangitis With Oral Vancomycin by the Study of Its Antimicrobial and Immunomodulating Effects
- Probiotics in Patients With Primary Sclerosing Cholangitis
- PSC Clinical Epidemiology in China
- Quality of Life in Patients With Primary Sclerosing Cholangitis
- Quantitative Magnetic Resonance Imaging in Biliary Disease: Health Economics Study
- Registry for Advanced Endoscopy
- Registry Trial to Determine pCLE Image Interpretation Criteria and Preliminary Accuracy for PSC Biliary Strictures
- Repeatability and Reproducibility of Multiparametric MRI
- Repeatability and Reproducibility of Quantitative MRCP
- Safety and Efficacy Study of Ursodeoxycholic Acid Therapy in Pediatric Primary Sclerosing Cholangitis
- Safety and Tolerability of A3907 in Primary Sclerosing Cholangitis
- Safety and Tolerability of Cilofexor in Participants With Primary Sclerosing Cholangitis (PSC) and Compensated Cirrhosis
- Safety, Tolerability, and Efficacy of Cilofexor in Adults With Primary Sclerosing Cholangitis Without Cirrhosis
- Safety, Tolerability, and Efficacy of Cilofexor in Non-Cirrhotic Adults With Primary Sclerosing Cholangitis
- Secondary Sclerosing Cholangitis in Critically Ill Patients
- Short-term Stenting Versus Balloon Dilatation for Dominant Strictures in Primary Sclerosing Cholangitis
- Simtuzumab (GS-6624) in the Prevention of Progression of Liver Fibrosis in Adults With Primary Sclerosing Cholangitis (PSC)
- SSC-COVID in Patients After COVID-19
- Study in Healthy Volunteers to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of CS0159
- Sulfasalazine for the Treatment of Primary Sclerosing Cholangitis
- Surgical Reconstruction in Ulcerative Colitis With Primary Sclerosing Cholangitis
- Surveillance Study for Early Detection of Cholangiocarcinoma (CCA) in Primary Sclerosing Cholangitis (PSC)
- Swiss Primary Sclerosing Cholangitis Cohort Study
- Telomere Length and Other Parameters of Telomere Dysfunction in PSC and Colitis
- Thalidomide for the Treatment of Primary Sclerosing Cholangitis (PSC)
- The Effect of Bezafibrate on Cholestatic Itch
- The Value of CT Cholangiography in Primary Sclerosing Cholangitis
- Treating Primary Sclerosing Cholangitis and Biliary Atresia With Vancomycin
- Trial of High-dose Urso in Primary Sclerosing Cholangitis
- Umbilical Cord Mesenchymal Stem Cells in Primary Sclerosing Cholangitis
- Unraveling the Mechanisms Underlying Primary Sclerosing Cholangitis Through a Multidisciplinary, Integrative Research Approach
- Vancomycin for Primary Sclerosing Cholangitis
- Vancomycin Treatment in Recurrent PSC in Liver Transplant Patients
- Vidofludimus Calcium for Primary Sclerosing Cholangitis
- Volumetric Laser Endomicroscopy’s (VLE) Diagnostic Accuracy Validation Study: Impact on Clinical Management Study
Clinical Trials
- Assessment of Photopill Capsule Treatment for Safety and Feasibility in Ulcerative Proctitis
- Budesonide vs. Mesalazine vs. Budesonide/Mesalazine Suppository Combination Therapy in Acute Ulcerative Proctitis
- Clinical Trial With Mesalamine 1g Suppositories
- Efficacy and Safety of Budesonide Foam for Participants With Active Mild to Moderate Ulcerative Proctitis or Proctosigmoiditis
- Efficacy and Safety of Budesonide Foam for Participants With Active Mild to Moderate Ulcerative Proctitis or Proctosigmoiditis
- Physical Fitness Levels in Children and Adolescents With Chronic Inflammatory Bowel Disease (CIBD): Crohn’s Disease, Ulcerative Colitis, Chronic Unclassified Colitis
- Suspicion of Non IgE-mediated Cow’s Milk Protein Allergy: Prevalence and Evolution
- The Safety and Tolerability of Budesonide Foam in Participants With Active Ulcerative Proctitis or Proctosigmoiditis
- A Study of Zoledronic Acid, Pravastatin, and Lonafarnib for Patients With Progeria
- Clinical Studies of Progeria
- Lonafarnib for Patients With Hutchinson-Gilford Progeria Syndrome or Progeroid Laminopathy
- Phase I Study of Progerinin in Healthy Volunteers
- Phase I/II Trial of Everolimus in Combination With Lonafarnib in Progeria
- Phase II Trial of Lonafarnib (a Farnesyltransferase Inhibitor) for Progeria
- Study of Zoledronic Acid, Pravastatin, and Lonafarnib for Patients With Progeria
- Treatment of the Hutchinson-Gilford Progeria Syndrome With a Combination of Pravastatin and Zoledronic Acid
- Umbilical Cord Blood Transfusion in Progeria Syndrome
- Clinical Trial Comparing Two Non-Surgical Treatments for Severe Blepharoptosis
- Genomic Profiling of Mitochondrial Disease – Imaging Analysis for Precise Mitochondrial Medicine
- MRI Study – Chronic Progressive External Ophthalmoplegia
- Nicotinamide Riboside and Mitochondrial Biogenesis
- The KHENEREXT Study
- A Placebo-controlled Study of Maralixibat (SHP625) in Pediatric Subjects With Progressive Familial Intrahepatic Cholestasis (PFIC)
- A Safety and Pharmakokinetic Study of A4250 Alone or in Combination With A3384
- A Study of TAK-625 for the Treatment of Progressive Familial Intrahepatic Cholestasis (PFIC)
- A Study to Evaluate the Safety and Tolerability of Maralixibat in Infant Participants With Cholestatic Liver Diseases Including Progressive Familial Intrahepatic Cholestasis (PFIC) and Alagille Syndrome (ALGS).
- An Open Label, Single-dose, Single Period ADME Study of A4250 in Healthy Subjects
- Buphenyl Therapy for Byler’s Disease
- Expanded Access Protocol for an Intermediate Size Population – RAVICTI for Byler Disease
- Gastrostomy-Biliary Diversion: Innovative Management for Bile Canalicular Transport Disorders
- Long Term Safety & Efficacy Study Evaluating The Effect of A4250 in Children With PFIC
- Longitudinal Study of Genetic Causes of Intrahepatic Cholestasis (LOGIC)
- Odevixibat for the Treatment of Progressive Familial Intrahepatic Cholestasis
- Open Label Study to Evaluate Efficacy and Long Term Safety of LUM001 in the Treatment of Cholestatic Liver Disease in Patients With Progressive Familial Intrahepatic Cholestasis
- Progressive Familial Intrahepatic Cholestasis in Indian Children – Establishing an Indian PFIC Registry
- Transition From Buphenyl to RAVICTI for the Therapy of Byler Disease
- Validation of the Itch Reported Outcome (ItchRO) Diaries in Pediatric Cholestatic Liver Disease
- A Study to Evaluate the Efficacy and Safety of Maralixibat in Subjects With Progressive Familial Intrahepatic Cholestasis (MARCH-PFIC)
- An Extension Study of Maralixibat in Patients With Progressive Familial Intrahepatic Cholestasis (PFIC)
- NAtural Course and Prognosis of PFIC and Effect of Biliary Diversion
- This Study Will Investigate the Efficacy and Safety of A4250 in Children With PFIC 1 or 2
- 18F-PM-PBB3 PET Study in Tauopathy Including Alzheimer’s Disease, Other Dementias and Normal Controls
- 2-(1-{6-[(2-[F-18]Fluoroethyl) (Methyl)Amino]-2-naphthyl} Ethylidene) Malononitrile-PET for in Vivo Diagnose of Tauopathy in Unclassified Parkinsonism
- 4 Repeat Tauopathy Neuroimaging Initiative
- 4-Repeat Tauopathy Neuroimaging Initiative – Cycle 2
- A 6 Month, Open-Label, Pilot Futility Clinical Trial of Oral Salsalate for Progressive Supranuclear Palsy
- A Molecular Anatomic Imaging Analysis of Tau in Progressive Supranuclear Palsy
- A Phase 2a Study of TPN-101 in Patients With Progressive Supranuclear Palsy (PSP)
- A Pilot Clinical Trial of Pyruvate, Creatine, and Niacinamide in Progressive Supranuclear Palsy.
- A Pilot Trial of Lithium in Subjects With Progressive Supranuclear Palsy or Corticobasal Degeneration
- A Study to Assess Efficacy, Safety, Tolerability, and Pharmacokinetics of ABBV-8E12 in Subjects With Progressive Supranuclear Palsy (PSP).
- A Study to Assess Tolerability, Safety, Pharmacokinetics and Effect of AZP2006 in Patients With PSP
- A Study to Evaluate the Diagnostic Efficacy of DaTSCAN™ Ioflupane (123I) Injection in Single Photon Emission Computed Tomography (SPECT) for the Diagnosis of Parkinsonian Syndrome (PS) in Chinese Patients
- A Study to Test the Safety and Tolerability of Long-term UCB0107 Administration in Study Participants With Progressive Supranuclear Palsy
- A Study to Test the Safety and Tolerability of UCB0107 in Study Participants With Progressive Supranuclear Palsy (PSP)
- ADDIA Proof-of-Performance Clinical Study
- Advancing Research and Treatment for Frontotemporal Lobar Degeneration (ARTFL)
- Alpha-lipoic Acid/L-acetyl Carnitine for Progressive Supranuclear Palsy
- An Extension Study of ABBV-8E12 in Progressive Supranuclear Palsy (PSP)
- Analysis of the Enteric Nervous System Using Colonic Biopsies
- Application od Machine Learning Method in Validation of Screening Cognitive Test for Parkinsonisms
- ARTFL LEFFTDS Longitudinal Frontotemporal Lobar Degeneration (ALLFTD)
- Biomarkers in Parkinsonian Syndromes
- Brain Network Activation in Patients With Movement Disorders
- Building Online Community for Parkinson’s Palliative Care
- Cerebellar rTMS Theta Burst for Postural Instability in Progressive Supranuclear Palsy
- Cholinergic Mechanisms of Attentional-motor Integration and Gait Dysfunction in Parkinson Disease (UDALL)
- Chromatic Pupillometry to Assess the Melanopsin-Light Pathway in Progressive Supranuclear Palsy
- Clinical Trial to Evaluate Bone Marrow Stem Cell Therapy for PSP, a Rare Form of Parkinsonism
- Complex Eye Movements in Parkinson’s Disease and Related Movement Disorders
- Continuously Infused Recombinant-Methionyl Human Glial Cell Line-Derived Neurotrophic Factor (GDNF) to Treat Progressive Supranuclear Palsy
- Davunetide (AL-108) in Predicted Tauopathies – Pilot Study
- Deep TMS for the Treatment of Patients With Parkinson’s Disease and Progressive Supranuclear Palsy
- Defining Phenotypes of Movement Disorders :Parkinson’s Plus Disorders (PD), Essential Tremor (ET), Cortical Basal Degeneration (CBD), Multiple Systems Atrophy (MSA), Magnetoencephalography.
- Diagnosing Frontotemporal Lobar Degeneration
- Diagnostic and Prognostic Biomarkers in Parkinson Disease
- Effects of Coenzyme Q10 in Progressive Supranuclear Palsy (PSP)
- Effects of Coenzyme Q10 in PSP and CBD
- Efficacy and Safety of Transcranial dIrect Current stiMulation (tDCS) in Progressive Supranuclear Palsy (PSP) (STIM-PSP)
- Efficacy Study for Treatment of Dementia in Progressive Supranuclear Palsy
- Efficacy, Tolerability and Safety of Azilect in Subjects With Progressive Supranuclear Palsy
- Evaluating Cerebrospinal Fluid Biomarkers in Alzheimer’s, Progressive Supranuclear Palsy Subjects, and Controls
- Evaluation of [18F]APN-1607 as a PET Biomarker
- Evaluation of [18F]MNI-777 PET as a Marker of Tau Pathology in Subjects With Tauopathies Compared to Healthy Subjects
- Evaluation of [18F]MNI-815 as a Potential PET Radioligand for Imaging Tau Protein in the Brain of Patients With Tauopathies
- Evaluation of [18F]MNI-952 as a Potential PET Radioligand for Imaging Tau Protein in the Brain
- Evaluation of Imaging Characteristics of [18F]PI-2620 PET in AD and PSP Patients Using High and Low Specific Activity
- Evaluation of the Efficacy of a Two-week EMST on Dysphagia in Parkinsonian Patients
- Evaluation of Tolfenamic Acid in Individuals With PSP at 12-Weeks
- Extension Study of ABBV-8E12 in Patients With Progressive Supranuclear Palsy (PSP) Who Completed Study C2N-8E12-WW-104
- Extension Study of BIIB092 in Participants With Progressive Supranuclear Palsy (PSP) Who Participated in CN002003
- Facilitating Diagnostics and Prognostics of Parkinsonian Syndromes Using Neuroimaging
- Foot Mechanical Stimulation for Treatment of Gait and Gait Related Disorders in Parkinson’s Disease and Progressive Supranuclear Palsy.
- Gait Analysis in Neurological Disease
- Human CNS Tau Kinetics in Tauopathies
- Identifying Biomarkers of Parkinson’s Disease Using Magnetic Resonance Imaging (MRI)
- Image Characteristic and Longitudinal Follow up of 18F-PMPBB3 (APN-1607) PET for Progressive Supranuclear Palsy
- In-Home Care for Patients With PSP and Related Disorders
- Investigating Complex Neurodegenerative Disorders Related to Amyotrophic Lateral Sclerosis and Frontotemporal Dementia
- Misfolded Proteins in the Skin of People With Parkinson’s Disease and Other Parkinsonism
- More Than a Movement Disorder: Applying Palliative Care to Parkinson’s Disease
- Multiple Ascending Dose Study of Intravenously Administered BMS-986168 (BIIB092) in Patients With Progressive Supranuclear Palsy
- Neurodegenerative Diseases Registry
- Neurologic Stem Cell Treatment Study
- Neuroprotection and Natural History in Parkinson’s Plus Syndromes (NNIPPS)
- Neuropsychological Evaluation for Early Diagnosis of PSP
- Optimization of Morphomer-based Alpha-synuclein PET Tracers
- Oxford Study of Quantification in Parkinsonism
- Pathophysiology of Gait and Posture in Progressive Supranuclear Palsy
- Personalized Parkinson Project PSP Cohort
- Phase 0 Evaluation of [18F]MNI-958 as a Potential PET Radioligand for Imaging Tau Protein in the Brain
- Phase 1 Test-retest Evaluation of [18F]MNI-958 PET
- Postural Instability in Progressive Supranuclear Palsy
- PROgressive Supranuclear Palsy CorTico-Basal Syndrome Multiple System Atrophy Longitudinal Study UK
- Quality of Life of the Patient and the Burden of the Caregiver in Progressive Supranuclear Palsy
- Rehabilitation in Patients With Progressive Supranuclear Palsy
- Remote Monitoring in Progressive Supranuclear Palsy (PSP)
- Repetitive Transcranial Magnetic Stimulation (TMS) for Progressive Supranuclear Palsy and Corticobasal Degeneration
- Research of Biomarkers in Parkinson Disease
- Rho Kinase (ROCK) Inhibitor in Tauopathies – 1
- Risk Factors for Progressive Supranuclear Palsy (PSP)
- Robot Walking Rehabilitation in Parkinson’s Disease
- RT001 in Patients With Progressive Supranuclear Palsy (PSP) PROGRESSIVE SUPRANUCLEAR PALSY
- Safety and Efficacy of Droxidopa for Fatigue in Patients With Parkinsonism
- Safety Study of TPI-287 to Treat CBS and PSP
- Safety, Tolerability and Pharmacokinetics of Multiple Ascending Doses of NIO752 in Progressive Supranuclear Palsy
- Safety, Tolerability, and Efficacy of Two Different Oral Doses of NP031112 Versus Placebo in the Treatment of Patients With Mild-to-Moderate Progressive Supranuclear Palsy
- Safety, Tolerability, and Pharmacokinetics of C2N-8E12 in Subjects With Progressive Supranuclear Palsy
- Study About Safety and Efficacy of Coenzyme Q10 in Progressive Supranuclear Palsy
- Study of BIIB092 in Participants With Progressive Supranuclear Palsy
- Study of Comprehensive ANd Multimodal Marker-based Cohort of Progressive Supranuclear Palsy(PSP)
- Study of NBMI Treatment in Patients With Atypical Parkinsons (PSP or MSA)
- Study of the Distractibility Syndrome in Patients With Progressive Supranuclear Palsy
- Study of the Neural Basis of Analogical Reasoning
- Study to Evaluate the Safety and Efficacy of Davunetide for the Treatment of Progressive Supranuclear Palsy
- Subcutaneous Apomorphine in the Treatment of Progressive Supranuclear Palsy and Cortico Basal Degeneration (APOPARKA)
- Systematic Assessment of Laryngopharyngeal Function in Patients With MSA, PD, and 4repeat Tauopathies
- Tau Imaging in Subjects With Progressive Supranuclear Palsy, Corticobasal Degeneration and Healthy Volunteers
- Tau Imaging With JNJ067
- Tau Protein and SV2a Imaging in Patients With Tau Protein-related Diseases
- tDCS and Speech Therapy for Motor Speech Disorders Caused by FTLD Syndromes: a Feasibility Study
- tDCS Plus Physical Therapy for Progressive Supranuclear Palsy
- Test-retest Study With [18F]PI-2620 in PSP-RS and NDC
- The MOTIVE-PSP Initiative
- The Neural Basis for Frontotemporal Degeneration
- The Study to Evaluate the Safety and Efficacy of Spinal Cord Stimulation on Progressive Supranuclear Palsy
- Transcranial Duplex Scanning and Single Photon Emission Computer Tomography (SPECT) in Parkinsonian Syndromes
- Transcranial Magnetic Stimulation in Progressive Supranuclear Palsy
- Trial of Parkinson’s And Zoledronic Acid
- Trial of Valproic Acid in Patients With Progressive Supranuclear Palsy (Depakine)
- Unstructured Eye Tracking as a Diagnostic and Prognostic Biomarker in Parkinsonian Disorders
- UPenn Observational Research Repository on Neurodegenerative Disease
- Young Plasma Transfusions for Progressive Supranuclear Palsy
- “The MaP Study”: Mapping the Patient Journey in MMA and PA
- A First in Human, Dose Escalation Study to Evaluate the Safety and Tolerability of BBP-671 in Healthy Volunteers and Patients With Propionic Acidemia or Methylmalonic Acidemia
- A Long-Term Extension Study to Evaluate the Safety and Clinical Activity of mRNA-3927
- A Retrospective Study to Characterize Participants With Propionic Acidemia
- Anaplerotic Therapy in Propionic Acidemia
- Carglumic Acid in Methylmalonic Acidemia and Propionic Acidemia
- Characterization of Intestinal Microbiota in Children With Inborn Errors of Metabolism (IEM)
- Increasing Ureagenesis in Inborn Errors of Metabolism With N-Carbamylglutamate
- Long-term Outcome of N-Carbamylglutamate Treatment in Propionic Acidemia and Methylmalonic Acidemia
- Natural History Study of Patients With Methylmalonic Acidemia and Propionic Acidemia
- Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia
- Open Label Study of mRNA-3927 in Patients With Propionic Acidemia
- Review of Charts From Amish/Mennonite Variant PA Patients
- Study of HST5040 in Subjects With Propionic or Methylmalonic Acidemia
- Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods Approach
- A Multi-Cohort Phase 2 Dose-Escalation Study of ARQ 092 (Miransertib) in Proteus Syndrome
- Dose Finding Trial of ARQ 092 in Children and Adults With Proteus Syndrome
- Expanded Access to Provide ARQ 092 for the Treatment of Overgrowth Diseases and/or Vascular Anomalies
- Informed Consent for Whole Genome Sequencing: Ideals and Norms Referenced by Early Participants
- Study of Proteus Syndrome and Related Congenital Disorders
- A Long-term Study of Nemolizumab (CD14152) in Participants With Prurigo Nodularis (PN)
- A Randomized Placebo-Controlled Study of the Neurokinin-1 (NK1) Receptor Antagonist Serlopitant Prurigo Nodularis (PN)
- A Study of CDX-0159 in Patients With Prurigo Nodularis
- A Study to Assess the Efficacy and Safety of Nemolizumab (CD14152) in Participants With Prurigo Nodularis (PN)
- A Study to Assess the Efficacy, Safety, and Tolerability of KPL-716 in Reducing Pruritus in Prurigo Nodularis
- A Study to Evaluate the Durability of Response and Safety of Nemolizumab for 24 Weeks in Participants With Prurigo Nodularis
- A Study to Evaluate the Efficacy and Safety of INCB054707 in Participants With Prurigo Nodularis
- A Study to Evaluate the Efficacy and Safety of Ruxolitinib Cream in Participants With Prurigo Nodularis (PN)
- An Efficacy and Safety Study of Nemolizumab (CD14152) in Participants With Prurigo Nodularis
- Apremilast as Anti-pruritic Treatment in Patients With Prurigo Nodularis
- China Type II Inflammatory Skin Disease Clinical Research and Standardized Diagnosis and Treatment Project
- Effectiveness of the Selective Serotonin Reuptake Inhibitor,Citalopram (Cipralex), in Prurigo Nodularis
- Efficacy of Abrocitinib for Reducing Pruritus in Adults With Prurigo Nodularis and Chronic Pruritus of Unknown Origin
- Evaluation of the Antipruritic Effect of Elidel (Pimecrolimus) in Non-atopic Pruritic Disease
- Expanded Access Use of Dupilumab
- Open Label Extension Study of Nalbuphine HCl ER in Patients With Prurigo Nodularis
- Pain Outcomes Following Intralesional Corticosteroid Injections
- PRISM Study-Pruritus Relief Through Itch Scratch Modulation
- Safety and Efficacy of CC-10004 for Prurigo Nodularis
- Safety and Efficacy of Nemolizumab in PN
- Study of Nalbuphine HCl ER Tablets in Patients With Prurigo Nodularis
- Study of the Efficacy, Safety and Tolerability of Serlopitant for the Treatment of Pruritus (Itch) With Prurigo Nodularis
- Study of the Efficacy, Safety and Tolerability of Serlopitant for the Treatment of Pruritus (Itch) With Prurigo Nodularis
- Study of the Long Term Safety of Serlopitant for the Treatment of Pruritus (Itch)
- Transcriptomic Landscape of T Lymphocytes of Atopic Dermatitis, Atopic Prurigo Nodularis (of Besnier) and Non-atopic Prurigo Nodularis (of Hyde) Using Single Cell RNA-sequencing