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  5. Patient Caregiver’s Journey in...

Patient Caregiver’s Journey in ASMD

January 5, 2018[email protected]
https://www.youtube.com/watch?v=6LMTnU0rI-s&list=PLmqBxf22n4lOwf-cR3LXbqYcBumYyyxJz&index=1

A mother of a patient with Acid Sphingomyelianse Deficiency (ASMD) talks about the journey she and her family had taken to help diagnose her son with ASMD. She highlights the support she has received from the National Niemann-Pick Disease Foundation and encourages further education in lysosomal storage disorders among the society.

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