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Rare disease spotlight


#OneRbWorld2021 Virtual has a NEW DATE: 1-3 October. We’re sad COVID keeps us apart again, but we promise you a very warm welcome and fully interactive program. Please save the NEW DATE, 1-3 Oct for immersive #retinoblastoma community and collaboration to advance care for all.

Proud to partner with #PatientAdvocacy organization @CureCRB1 in our 2021 Young Investigator Draft to co-fund important research for the #RareDisease community! #WeTackleRare

New #webinar: "Transitioning to Adult Care” on April 21 at 2:00pm ET. Join #NORD to learn how to plan for the transition from parent-supervised pediatric care to more independent adult care. #rarediseases Register:

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