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Paris, France – GenSight Biologics (Euronext: SIGHT, ISIN: FR0013183985, PEA-PME eligible), a biopharma company focused on discovering and developing innovative gene therapies for retinal neurodegenerative diseases and central nervous system disorders, today reported that Leber Hereditary Optical Neuropathy (LHON) subjects treated with LUMEVOQ® continued to experience significantly improved vision four... -
CAMBRIDGE, Mass. – Alnylam Pharmaceuticals, Inc. (Nasdaq: ALNY), the leading RNAi therapeutics company, announced today that the HELIOS-A Phase 3 study of vutrisiran, an investigational RNAi therapeutic in development for the treatment of transthyretin-mediated (ATTR) amyloidosis, met all secondary endpoints measured at 18 months in patients with hATTR amyloidosis with...
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NEW YORK & MIAMI – Pfizer Inc. (NYSE: PFE) and OPKO Health, Inc. (NASDAQ: OPK) announced today that the U.S. Food and Drug Administration (FDA) issued a Complete Response Letter (CRL) for the Biologics License Application (BLA) for somatrogon. Somatrogon is an investigational once-weekly long-acting recombinant human growth hormone for...
Videos
Rare disease spotlight
https://www.theatlantic.com/science/archive/2021/12/mask-guidelines-cdc-walensky/621035/
Walensky at Senate Hearing yesterday still citing 3.5X figure. This is per a school mask study that my @TheAtlantic investigation revealed contains >40 schools *that don't exist*, and studied schools without mask mandates *longer* than those with mandates https://www.c-span.org/video/?c4995967/user-clip-walensky-35x-111
Why are triple vaxxed, healthy 20 year olds still forced to wear masks, along with many other restrictions on campus?
Impassioned thread by a professor, quoting from her @BostonGlobe op-ed, for colleges to bring back normalcy for students *now*
https://www.bostonglobe.com/2022/01/20/opinion/college-covid-restrictions-have-become-overkill/
