Latest News
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PARIS, France and CAMBRIDGE, MA, USA – Sanofi and Alnylam Pharmaceuticals, Inc. (Nasdaq: ALNY), the leading RNAi therapeutics company, announced a strategic restructuring of their RNAi therapeutics alliance to streamline and optimize development and commercialization of certain products for the treatment of rare genetic diseases. Specifically: Sanofi will obtain global development and commercialization rights... -
VANCOUVER, British Columbia – Zymeworks Inc. (NYSE/TSX: ZYME), a clinical-stage biopharmaceutical company developing next-generation multifunctional biotherapeutics, provided key accomplishments from the past year and announced priorities for 2018. “2017 was a great year for Zymeworks and we are poised to achieve a number of important corporate milestones in 2018,” said Ali Tehrani,...
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Alzheimer’s disease is a devastating brain illness that affects an estimated 47 million people worldwide. It is the most common cause of dementia in the Western world. Despite this, there are currently no treatments that are effective in curing Alzheimer’s disease or preventing its relentless progression. Alzheimer’s disease is caused...
Videos
Rare disease spotlight
Wellness & Well-Being is the #aHUSday 2020 theme. Connections? Getting Back to Normal: #aHUS registry data on Patient Reported Outcomes (PROs) What’s the scoop on fatigue, #dialysis, plasma therapies & other PROs? 4th in our series, #PatientExperiences https://www.ahusallianceaction.org/how-are-you-doing-part-4-pro-data-in-use/
One of the "extremely high #costs" is the #impact on #RareDiseases.
There’s an elephant in the room missing from this conversation @BBCNewsnight. The highest risk group for both death and hospitalisation from #COVID19 is those who have metabolic syndrome. That’s 1 in 4 adults in UK and likely includes huge numbers of doctors and nurses too! https://twitter.com/bbcquestiontime/status/1306720401356095492
Only a few hours to go until our BPA Connect 2020 event!
If you haven't registered, please do so by midnight tonight, your Zoom links and Information Packs will be emailed in the morning.
Looking forward to seeing you then :)
https://www.eventbrite.co.uk/e/bpa-connect-2020-online-live-together-tickets-112891842540
#BPAConnect2020 https://twitter.com/BPA_Porphyria/status/1304762749705244672
I've just posted all the Info Packs out to UK, Isle of Man and Ireland postcodes... you should all receive them soon.... we'll be sharing all this info electronically for all attendees incl. non-UK residents.
There's still time to register for electronic information. https://twitter.com/BPA_Porphyria/status/1303361090890407938