AUSTIN, Texas — Frances Arnold, PhD, winner of the 2018 Nobel Prize in Chemistry, has been awarded a two-year grant by the Foundation for Angelman Syndrome Therapeutics (FAST) to develop new molecular tools that could help advance future RNA-targeted therapeutics for Angelman syndrome. The project will apply directed evolution, the...

SANTA CRUZ, California – New Living with Lambert-Eaton Myasthenic Syndrome (LEMS), a rare autoimmune disorder affecting the nerves and muscles, often requires seeing multiple specialists to help with your condition. That’s partly because 50 percent to 60 percent of cases are paraneoplastic, meaning they co-occur with cancer, particularly small-cell lung...

COLUMBUS, Ohio — Andelyn Biosciences Inc., a patient-focused cell and gene therapy Contract Development and Manufacturing Organization (CDMO), today announced the unveiling of The Andelyn Foundation, a nonprofit organization dedicated to supporting families living with rare and ultra-rare diseases through awareness, fundraising, and compassionate community engagement. More than 10,000 rare diseases have...