Ottawa, Canada – Georges Wistaff calls CHEO his family’s second home. They have made more than 100 trips there over the last decade, mostly because of health issues involving their 10-year-old son, Antony. Antony was born prematurely and underwent emergency surgery soon after. That was the start of a medical...

NORTH BETHESDA, Md. — The Foundation for the National Institutes of Health (FNIH) announces the launch of a public-private partnership to build the largest data source for amyotrophic lateral sclerosis (ALS) and expedite the identification of biomarkers and clinical outcome assessments that would allow earlier diagnosis and accelerated drug development...

ORLANDO, Florida — Until Susan Caldwell of Waxahachie, Texas, learned in 2016 that her 8-year-old son Ryan Michael had Duchenne muscular dystrophy (DMD), she had never heard of the disease—and only vaguely knew of muscular dystrophy, thanks to the Jerry Lewis Telethon. “It was devastating,” she recalled. “I had met...