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Rare disease spotlight


Are you an advocate for people living with a rare disease? Take our free online training and learn how to:

☑️ Create empowered communities
☑️ Build effective channels and reach the right people.

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Help raise awareness of and support #RareDisease at the virtual #RAREsummit21 brought to you by @Camraredisease on 7 October 2021. Agenda, tickets and more info at

Thank you Senator @JimInhofe for cosponsoring the #ACTforALS (S. 1813), which would speed up therapies for the #NMD community, including those living with #ALS! #EndALS

This Fact Friday we are highlighting studies on DMD affected females! Check out these interesting quotes from 2 research articles on DMD carriers. #Duchenne #MuscularDystrophy #RareDisease #NotJustCarriers #DMD

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