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Rare disease spotlight


ICYMI: During XLH Week we talked about the Transitions Toolkit, a collaboration between Quinnipiac University, Ultragenyx and The XLH Network, Inc.. The toolkit is available for download at our website:

We’re honored to receive the @Rarediseases 2020 Industry Innovation Award at this year’s #RareImpact Awards. Our commitment to reimagining medicine has led to innovative treatments for children like Malachi, who has #SpinalMuscularAtrophy (SMA) Type 1.

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