Latest News
-
BEDFORD, Mass. – Stoke Therapeutics, Inc, a new company working to increase gene expression to treat a wide array of diseases caused by genetic insufficiency, announced that it has completed a $40 million Series A financing to support the further advancement of multiple pre-clinical development programs. The Series A round...
Videos
Rare disease spotlight
Rare Disease advocates from (L) Kenya 🇰🇪, Tanzania 🇹🇿, Zimbabwe 🇿🇼, Ghana 🇬ðŸ‡
Creating awareness in Africa! https://twitter.com/cmutena/status/1291335970051305473
@georgemsengi @raddafoundation @Psalmy_Bizzle
This was a fun night!!!
Keep safe!
Keep connected with #aHUS news and articles with the aHUS Global Advocate, including highlights from national groups and research teams around the world. FMI & link to get your free copies today:
https://www.ahusallianceaction.org/keeping-ahus-connected/ Thanks for your Support! #aHUS24Sept @aHUS24Sept #SHUa
This is great! Please keep sharing your experience using #RareAcrossAmerica https://twitter.com/BarbyIngle/status/1290710186429001731
Thank you Senator @kyrstensinema & Sylvia, legislative advocate for being active in the Rare Disease Caucus and caring about us (700K+ Arizonians) living with a #RareDissease. #NIHFunding #NewbornScreenings #AccessToCare We appreciate your continued support! #RareAcrossAmerica