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BEDFORD, Mass. – Stoke Therapeutics, Inc, a new company working to increase gene expression to treat a wide array of diseases caused by genetic insufficiency, announced that it has completed a $40 million Series A financing to support the further advancement of multiple pre-clinical development programs. The Series A round...
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Rare disease spotlight
Looking forward to hearing all the research progress. https://twitter.com/CNSdrughunter/status/1315639287032012800
The #CDKL5 Forum annual meeting is staring right now! It would have been London this year, but it is obviously online. I am very much looking forward to all of the preclinical and clinical presentations in these 3 days!!!!
Living with a rare disease can be tough... if you're finding things harder than usual, reach out to someone else for help/support. https://twitter.com/MindCharity/status/1314808670975389696
Today is #WorldMentalHealthDay. Do one thing today for better mental health, whether it’s reaching out for support, or helping someone else. Start here > https://bit.ly/2SF3YA3 #DoOneThing