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  • The classic symptoms of Parkinson’s disease involve tremor, stiffness and slow movements. Over the last decade, neurologists have been paying greater attention to non-motor symptoms, such as digestive and sleep problems, loss of sense of smell and depression. A genetically engineered mouse reproduces many of the non-motor symptoms associated with...
  • MADISON — A fundamental question about how sugar units are strung together into long carbohydrate chains has also pinpointed a promising way to target new medicines against tuberculosis. Working with components of the tuberculosis bacterium, researchers from the University of Wisconsin-Madison identified an unusual process by which the pathogen builds...
  • Amsterdam – Collaboration in prostate cancer translational research in Europe is not only vital to sustain the progress achieved in recent years but also to streamline current efforts between researchers and clinicians and avoid duplication or overlaps. This was amongst the goals of the two-day Prostate Cancer Translational Research in...

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To save the 352,400 patients diagnosed each year in the USA with rare or orphan cancers we must save small biotech firms who provide these drugs. The SEC needs to GET SHORTY! @RareDiseases #mmsm @CheckOrphan @rarediseasefdn @SEC_Enforcement @SteveFDA

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ICYMI: During XLH Week we talked about the Transitions Toolkit, a collaboration between Quinnipiac University, Ultragenyx and The XLH Network, Inc.. The toolkit is available for download at our website: https://xlhnetwork.org/xlh-resources

We’re honored to receive the @Rarediseases 2020 Industry Innovation Award at this year’s #RareImpact Awards. Our commitment to reimagining medicine has led to innovative treatments for children like Malachi, who has #SpinalMuscularAtrophy (SMA) Type 1.

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