Brief Title
German Pediatric Hemophilia Research Database
Official Title
German Pediatric Hemophilia Research Database
Brief Summary
The German Pediatric Hemophilia Research Database will collect data on the prophylactic and therapeutic use of factor concentrates, complications, outcome measures (joint scores, QoL) and living circumstances in newly diagnosed children with hemophilia.
Study Type
Observational [Patient Registry]
Primary Outcome
Number of patients with antibody developement to exogenous clotting factors (>0.5 BU)
Condition
Hemophilia A
Intervention
documentation only
Study Arms / Comparison Groups
newly diagnosed children with hemophilia
Description: no intervention
Publications
* Includes publications given by the data provider as well as publications identified by National Clinical Trials Identifier (NCT ID) in Medline.
Recruitment Information
Recruitment Status
Other
Estimated Enrollment
200
Start Date
January 1, 2017
Completion Date
January 1, 2022
Primary Completion Date
January 1, 2022
Eligibility Criteria
Inclusion Criteria: - hemophilia A or B - FVIII/FIX <1% to 25% - informed consent Exclusion Criteria: - no consent
Gender
All
Ages
N/A - 18 Years
Accepts Healthy Volunteers
No
Contacts
Christoph Bidlingmaier, MD, +498944005, [email protected]
Location Countries
Germany
Location Countries
Germany
Administrative Informations
NCT ID
NCT02912143
Organization ID
GEPHARD
Secondary IDs
DRKS00011101
Responsible Party
Principal Investigator
Study Sponsor
Ludwig-Maximilians - University of Munich
Collaborators
Pediatric Committee of the German Thrombosis and Hemostasis Research Society
Study Sponsor
Christoph Bidlingmaier, MD, Principal Investigator, Pediatric Hemophilia Center, Dr. v. Hauner Children's Hospital, University of Munich
Verification Date
March 2018