- GlaxoSmithKline – Hypereosinophilic Syndrome
Sponsor: GlaxoSmithKline
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- M. Louise Markert – Immune defect due to absence of thymus
Sponsor: M. Louise Markert
- Joanne Kurtzberg, MD – Inborn amino acid metabolism disorder
Sponsor: Joanne Kurtzberg, MD
- Celldex Therapeutics – Metastatic gpNMB Expressing Triple Negative Breast Cancer
Sponsor: Celldex Therapeutics - Dana-Farber Cancer Institute – Multiple Myeloma in Relapse
Sponsor: Dana-Farber Cancer Institute - Eli Lilly and Company – Chronic Atypical Neutrophilic Dermatosis With Lipodystrophy and Elevated Temperature (CANDLE)
Sponsor: Eli Lilly and Company - Fudan University – Triple Negative Breast Cancer
Sponsor: Fudan University - Genentech, Inc. – Multiple Sclerosis
Sponsor: Genentech, Inc. - Hospital for Special Surgery, New York – Arthroplasty of the PIP Joint
Sponsor: Hospital for Special Surgery, New York - Kristin Fiorino – Refractory Gastroesophageal Reflux Disease With Upper Gastrointestinal (GI) Symptoms, Gastroparesis, and Chronic Constipation
Sponsor: Kristin Fiorino - National Taiwan University Hospital – Hyperlipidemia
Sponsor: National Taiwan University Hospital - University of Washington – Triple-Negative Breast Cancer
Sponsor: University of Washington - Zimmer Biomet – Peripheral Arterial Disease
Sponsor: Zimmer Biomet - Zimmer Biomet – Peripheral Vascular Diseases
Sponsor: Zimmer Biomet
- British Columbia Cancer Agency – Insulinoma
Sponsor: British Columbia Cancer Agency - Children’s Hospital of Philadelphia – Insulinoma
Sponsor: Children's Hospital of Philadelphia
- Stephen Trokel – Keratoconus
Sponsor: Stephen Trokel
- Catalyst Pharmaceutical Partners, Inc – Lambert-Eaton Myasthenic Syndrome
Sponsor: Catalyst Pharmaceutical Partners, Inc - Catalyst Pharmaceuticals, Inc. – Lambert-Eaton Myasthenic Syndrome
Sponsor: Catalyst Pharmaceuticals, Inc. - David Lacomis – Lambert-Eaton Myasthenic Syndrome
Sponsor: David Lacomis - Ricardo Maselli – Lambert-Eaton Myasthenic Syndrome
Sponsor: Ricardo Maselli - Tessa L Marburger – Lambert-Eaton Myasthenic Syndrome
Sponsor: Tessa L Marburger - The Cleveland Clinic – Lambert-Eaton Myasthenic Syndrome
Sponsor: The Cleveland Clinic - University of Colorado, Denver – Lambert-Eaton Myasthenic Syndrome
Sponsor: University of Colorado, Denver - University of Pittsburgh – Lambert-Eaton Myasthenic Syndrome
Sponsor: University of Pittsburgh - Vern C. Juel, M.D. – Lambert-Eaton Myasthenic Syndrome
Sponsor: Vern C. Juel, M.D.
- BioMarin Pharmaceutical – CLN2 Disease
Sponsor: BioMarin Pharmaceutical
- Chin-Hung Chang – Mesenchymal Stem Cells
Sponsor: Chin-Hung Chang - University of Nebraska – Evaluation of Troponin I Levels
Sponsor: University of Nebraska
- U.S. Army Medical Research and Materiel Command – Leishmaniasis
Sponsor: U.S. Army Medical Research and Materiel Command - U.S. Army Medical Research and Materiel Command – Leishmaniasis, Cutaneous
Sponsor: U.S. Army Medical Research and Materiel Command - Universidad Peruana Cayetano Heredia – Cutaneous Leishmaniasis
Sponsor: Universidad Peruana Cayetano Heredia - University of California, San Francisco – Leishmaniasis
Sponsor: University of California, San Francisco - University of California, San Francisco – Leishmaniasis, Cutaneous
Sponsor: University of California, San Francisco - University of California, San Francisco – Leishmaniasis, Mucocutaneous
Sponsor: University of California, San Francisco
- Cytori Therapeutics – Limited systemic sclerosis
Partner: Idis Sponsor: Cytori Therapeutics
- David P. Richman, MD – Lambert Eaton Myasthenic Syndrome
Sponsor: David P. Richman, MD - La Jolla Pharmaceutical Company – Catecholamine Resistant Hypotension (CRH)
Sponsor: La Jolla Pharmaceutical Company - Tessa L Marburger – Lambert-Eaton Myasthenic Syndrome (LEMS)
Sponsor: Tessa L Marburger - University of California, Davis – Lambert Eaton Myasthenic Syndrome
Sponsor: University of California, Davis - University of Colorado, Denver – Lambert Eaton Myasthenic Syndrome
Sponsor: University of Colorado, Denver - Vern C. Juel, M.D. – Lambert Eaton Myasthenic Syndrome (LEMS)
Sponsor: Vern C. Juel, M.D.
- AstraZeneca – NF type1 With Inoperable Plexiform Neurofibromas
Sponsor: AstraZeneca - University of California, San Francisco – Lymphomas
Sponsor: University of California, San Francisco
- Andrei Iagaru – Thyroid cancer- medullary
Sponsor: Andrei Iagaru - Johannes Czernin – Thyroid cancer- medullary
Sponsor: Johannes Czernin - Jonsson Comprehensive Cancer Center – Medullary Thyroid Cancer
Sponsor: Jonsson Comprehensive Cancer Center
- Merck KGaA – Metastatic Merkel Cell Carcinoma
Sponsor: Merck KGaA
- Bristol-Myers Squibb – Metastatic Melanoma
Sponsor: Bristol-Myers Squibb - Bristol-Myers Squibb – Metastatic Melanoma
Sponsor: Bristol-Myers Squibb - Eli Lilly and Company – Metastatic Melanoma
Sponsor: Eli Lilly and Company - Merck Sharp & Dohme Corp. – Metastatic Melanoma
Sponsor: Merck Sharp & Dohme Corp.
- Basilea Pharmaceutica – Mucormycosis
Partner: Idis Sponsor: Basilea Pharmaceutica
- AbbVie – Multiple Myeloma
Sponsor: AbbVie - Bristol-Myers Squibb – Multiple Myeloma
Sponsor: Bristol-Myers Squibb - Dana-Farber Cancer Institute – Multiple Myeloma
Sponsor: Dana-Farber Cancer Institute - Janssen Research & Development, LLC – Multiple Myeloma
Sponsor: Janssen Research & Development, LLC - Novartis Pharmaceuticals – Multiple Myeloma
Sponsor: Novartis Pharmaceuticals - Onyx Pharmaceuticals, Inc., an Amgen subsidiary – Multiple myeloma
Partner: Idis Sponsor: Onyx Pharmaceuticals, Inc., an Amgen subsidiary - Peking University – Multiple Myeloma
Sponsor: Peking University
- Emory University – Myelodysplastic syndromes
Sponsor: Emory University - University of California, San Francisco – Myelodysplastic syndromes
Sponsor: University of California, San Francisco
- Novartis Pharmaceuticals – Myelofibrosis
Sponsor: Novartis Pharmaceuticals
- Massachusetts General Hospital – Healthy Naturally Cycling Women
Sponsor: Massachusetts General Hospital
- InfaCare Pharmaceuticals Corporation – Hyperbilirubinemia transient familial neonatal
Sponsor: InfaCare Pharmaceuticals Corporation
- Apeiron Biologics AG – Neuroblastoma
Partner: Idis Sponsor: Apeiron Biologics AG - British Columbia Cancer Agency – Neuroblastoma
Sponsor: British Columbia Cancer Agency - Catalyst Pharmaceuticals, Inc. – Downbeat Nystagmus
Sponsor: Catalyst Pharmaceuticals, Inc. - Children’s Hospital Medical Center, Cincinnati – Neuroblastoma
Sponsor: Children's Hospital Medical Center, Cincinnati - Children’s Hospital of Philadelphia – Neuroblastoma
Sponsor: Children's Hospital of Philadelphia - Jubilant DraxImage Inc. – Neuroblastoma
Sponsor: Jubilant DraxImage Inc. - South Plains Oncology Consortium – Neuroblastoma
Sponsor: South Plains Oncology Consortium - South Plains Oncology Consortium – Neuroblastoma
Sponsor: South Plains Oncology Consortium - South Plains Oncology Consortium – Recurrent Neuroblastoma
Sponsor: South Plains Oncology Consortium - University of California, San Francisco – Neuroblastoma
Sponsor: University of California, San Francisco
- Center Trials & Treatment – Melanoma (Skin)
Sponsor: Center Trials & Treatment - Center Trials & Treatment – Melanoma Recurrent
Sponsor: Center Trials & Treatment - M. Louise Markert – Complete DiGeorge Anomaly
Sponsor: M. Louise Markert
- Vanda Pharmaceuticals Inc. – Non-24-hour Sleep Wake Disorder
Partner: Idis Sponsor: Vanda Pharmaceuticals Inc.
- Ariad Pharmaceuticals – Non-small Cell Lung Cancer
Sponsor: Ariad Pharmaceuticals
- Catalyst Pharmaceutical Partners, Inc – Nystagmus- congenital motor- autosomal recessive
Sponsor: Catalyst Pharmaceutical Partners, Inc
- Seoul National University Hospital – Ocular Cicatricial Pemphigoid
Sponsor: Seoul National University Hospital
- ArQule – PIK3CA-Related Overgrowth Spectrum (PROS)
Sponsor: ArQule - Astellas Pharma Global Development, Inc. – FMS-like Tyrosine Kinase-3 (FLT3) Mutations
Sponsor: Astellas Pharma Global Development, Inc. - Atara Biotherapeutics – Epstein-Barr Virus-Related Post-Transplant Lymphoproliferative Disorder
Sponsor: Atara Biotherapeutics - Eli Lilly and Company – Juvenile Dermatomyositis (JDM)
Sponsor: Eli Lilly and Company - Gerard Vockley, MD, PhD – Glucose Transporter 1 Deficiency Syndrome
Sponsor: Gerard Vockley, MD, PhD - Impatients N.V. trading as myTomorrows – Graft Vs Host Disease
Sponsor: Impatients N.V. trading as myTomorrows - Jonsson Comprehensive Cancer Center – Progressive Metastatic Castrate Resistant Prostate Cancer
Sponsor: Jonsson Comprehensive Cancer Center - Jonsson Comprehensive Cancer Center – Prostate Cancer
Sponsor: Jonsson Comprehensive Cancer Center - Loxo Oncology, Inc. – Neurotrophic Tyrosine Kinase, Receptor-related Proteins
Sponsor: Loxo Oncology, Inc. - MacroGenics – HER2-positive Breast Cancer
Sponsor: MacroGenics - Memorial Sloan Kettering Cancer Center – Prostate Cancer
Sponsor: Memorial Sloan Kettering Cancer Center - Memorial Sloan Kettering Cancer Center – Recurrent Prostate Cancer
Sponsor: Memorial Sloan Kettering Cancer Center - Novartis Pharmaceuticals – FLT3 Mutation, Internal Tandem Duplication (ITD) or Tyrosine Kinase Domain (TKD)
Sponsor: Novartis Pharmaceuticals - Pfizer – CD33 Positive Acute Myelogenous Leukemia
Sponsor: Pfizer - Reginald Dusing, MD – Prostate Cancer
Sponsor: Reginald Dusing, MD - Weill Medical College of Cornell University – Immunosuppression
Sponsor: Weill Medical College of Cornell University - Wendell Yap, MD – Prostate Cancer
Sponsor: Wendell Yap, MD - Xiaofan Zhu – Autosomal or Sex Linked Recessive Genetic Disease
Sponsor: Xiaofan Zhu - Zhejiang University – Stoma Closure Technic
Sponsor: Zhejiang University
- La Jolla Pharmaceutical Company – Vasodilatory Shock
Sponsor: La Jolla Pharmaceutical Company - Meir Medical Center – Percentage Body-Weight
Sponsor: Meir Medical Center - Seattle Genetics, Inc. – Disease, Hodgkin
Sponsor: Seattle Genetics, Inc. - University of California, Los Angeles – Refractory Childhood Epilepsy
Sponsor: University of California, Los Angeles