Catalyst Pharmaceuticals, Inc. – Downbeat Nystagmus

Access Program Information

The primary objective of the study is:

• To provide patients with LEMS/CMS/downbeat nystagmus access to amifampridine phosphate
therapy until the product becomes commercially available.

The secondary objective of the study is:

• To assess the long-term safety of amifampridine phosphate in patients with
LEMS/CMS/downbeat nystagmus

Rare Disease: