Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Country Product Indication Sponsor Date
Mazindol Narcolepsy HAC Pharma February 12, 2015
Sevuparin sodium Sickle cell anemia Modus Therapeutics AB February 12, 2015
N-[5-(3,5-difluorobenzyl)-1H-indazol-3-yl]-4-(4-methylpiperazin-1yl)-2-(tetrahydro-2H-pyran-4-ylamino)benzamide TrkA-positive, TrkB-positive, TrkC-positive, ROS1-positive, or ALK-positive colorectal cancer Ignyta, Inc.;11095 Flintkote Avenue, Suite D;San Diego, CA, 92121 February 12, 2015
N-(3-(4-(3-(diisobutylamino)propyl)piperazin-1-yl)propyl)-1H-benzo[d]imidazol-2-amine disulphate salt Progressive supranuclear palsy AlzProtect sas February 12, 2015
5-hydroxymethyl-2-furfural Sickle cell anemia Baxalta Innovations GmbH February 12, 2015
Alvocidib Acute myeloid leukaemia Theorem Clinical Research GmbH February 12, 2015
Allogeneic CD4+ and CD8+ T lymphocytes ex vivo incubated with synthetic peptides of the viral antigens of cytomegalovirus, adenovirus and Epstein-Barr virus Cytomegalovirus infection following haematopoietic stem cell transplantation Miltenyi Biotec GmbH February 12, 2015
Nitroglycerin Systemic scleroderma Covis Pharma S.à.r.l. February 12, 2015
Ulocuplumab Acute myeloid leukaemia Bristol-Myers Squibb Pharma EEIG February 12, 2015
Lactobacillus reuteri Prevention of necrotising enterocolitis Infant Bacterial Therapeutics AB February 12, 2015
N-[5-(3,5-difluorobenzyl)-1H-indazol-3-yl]-4-(4-methylpiperazin-1yl)-2-(tetrahydro-2H-pyran-4-ylamino)benzamide TrkA-positive, TrkB-positive, TrkC-positive, ROS1-positive, or ALK-positive colorectal cancer Ignyta, Inc.;4545 Towne Centre Court;San Diego, California, 92121 February 12, 2015
505 amino acid protein, corresponding to amino acids 2-506 of the wild type human histidyl-tRNA synthetase Facioscapulohumeral muscular dystrophy Voisin Consulting S.A.R.L. February 12, 2015
Olaratumab Soft tissue sarcoma Eli Lilly Nederland B.V. February 12, 2015
Defactinib Ovarian cancer Verastem, Inc.;117 Kendrick Street, Suite 500;Needham, Massachusetts, 02494 February 12, 2015
Myriocin Retinitis pigmentosa Nanovector s.r.l. February 12, 2015
Recombinant humanized anti-interleukin 13 (IL-13) monoclonal antibody Eosinophilic esophagitis Eosinophilic esophagitis Celgene Corporation;3033 Science Park Road, Suite 300;San Diego, California, 92121 February 11, 2015
3-pentylbenzenacetic acid sodium salt Idiopathic pulmonary fibrosis ProMetic Life Sciences, Inc.;440 Blvd Armand Frappier, Laval, Quebec, H7V 4B4; February 11, 2015
Pelareorep Pancreatic Cancer Oncolytics Biotech, Inc.;210, 1167 Kensington Crescent NW, Calgary AB T2N1X7; February 11, 2015
Glycyl-L-2-methylpropyl-L-glutamic acid Rett syndrome Neuren Pharmaceuticals, Ltd.;Level 1, 57 Wellington Street, Auckland 1011; February 11, 2015
Paromomycin Leishmaniasis The Surgeon General, Dept. of the Army;USAMRMC, 504 Scott Street;Ft. Detrick, Maryland, 21702 February 11, 2015
Pelareorep Ovarian cancer Oncolytics Biotech, Inc.;210, 1167 Kensington Crescent NW, Calgary AB T2N1X7; February 10, 2015
Carboxy pyrrolidine hexanoyl pyrrolidine carboxylate AL amyloidosis Glaxo Group Limited, England d/b/a GlaxoSmithKline;980 Great West Road, Middlesex, TW8 9GS; February 10, 2015
5-[8-methyl-9-(1-methylethyl)-2-(4-morpholinyl)-9H-purin-6yl]-2-pyrimidinamine Malignant pleural mesothelioma Verastem, Inc.;117 Kendrick Street, Suite 500;Needham, Massachusetts, 02494 February 10, 2015
Levomefolate calcium Megaloblastic anemia Cox Biosciences LLC;267 West 71st Street, #3F;New York, New York, 10023 February 10, 2015
Omeprazole-lansoprazole with buffer Esophageal ulcers Effexus Pharmaceuticals, LLC;10901 Granada Lane, Suite 101;Leawood, Kansas, 66211 February 10, 2015