Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Country Product Indication Sponsor Date
Cantrixil Ovarian cancer Kazia Therapeutics Limited;20 George Street, Suite 207;Hornsby April 20, 2015
177-LU-DOTA-GlyGlyNle-CycMSHhex Metastatic Melanoma SolaranRx, Inc.;5901 Indian School Road, NE;Albuquerque, New Mexico, 87110 April 16, 2015
2-[4-[[(2-R)-2-ethoxy-3-[4-(trifluoromethyl)phenoxy]propyl]thio]-2-methylphenoxy]acetic acid (1:1) lysine dihydrate Patients with Frederickson Type I or V hyperlipoproteinemia CymaBay Therapeutics, Inc.;7999 Gateway Blvd, Suite 130;Newark, California, 94560 April 15, 2015
Pelareorep Glioma Oncolytics Biotech, Inc.;210, 1167 Kensington Crescent NW, Calgary AB T2N1X7; April 15, 2015
[α⿿N-(2⿿succinyl-paclitaxel)Thr]-Phe-Phe-Tyr-Gly-Gly-Ser-Arg-Gly-[ε⿿N-(2⿿succinyl-paclitaxel)Lys]-Arg-Asn-Asn-Phe-[ε⿿N-(2⿿succinyl-paclitaxel)Lys]-Thr-Glu-Glu-Tyr Breast cancer patients with brain metastases Angiochem, Inc.;201 President Kennedy, Montreal, Quebec H2X 3Y7; April 15, 2015
Obinutuzumab Follicular lymphoma Genentech, Inc.;1 DNA Way;South San Francisco, California, 94080 April 15, 2015
Selumetinib Uveal melanoma AstraZeneca Pharmaceuticals LP;1800 Concord Pike, P. O. Box 8355;Wilmington, Delaware, 19803 April 15, 2015
Triheptanoin Fatty acid oxidation disorders Ultragenyx Pharmaceutical, Inc.;60 Leveroni Court;Novato, California, 94949 April 15, 2015
[α−N-(2’succinyl-paclitaxel)Thr]-Phe-Phe-Tyr-Gly-Gly-Ser-Arg-Gly-[ε−N-(2’succinyl-paclitaxel)Lys]-Arg-Asn-Asn-Phe-[ε−N-(2’succinyl-paclitaxel)Lys]-Thr-Glu-Glu-Tyr Breast cancer patients with brain metastases Angiochem, Inc.;201 President Kennedy, Montreal, Quebec H2X 3Y7; April 15, 2015
Diphenylcyclopropenone gel Metastatic Melanoma RXi Pharmaceuticals Corp.;257 Simarano Drive, Suite 101;Marlborough, Massachusetts, 01752 April 15, 2015
Zoledronate D,L-lysine monohydrate (ZLM) Reflex sympathetic dystrophy syndrome Grunenthal USA, Inc.;360 Mount Kemble Ave;Morristown, New Jersey, 07960 April 15, 2015
[α⿿N-(2⿿succinyl-paclitaxel)Thr]-Phe-Phe-Tyr-Gly-Gly-Ser-Arg-Gly-[ε⿿N-(2⿿succinyl-paclitaxel)Lys]-Arg-Asn-Asn-Phe-[ε⿿N-(2⿿succinyl-paclitaxel)Lys]-Thr-Glu-Glu-Tyr Breast cancer patients with brain metastases Angiochem, Inc.;201 President Kennedy, Montreal, Quebec H2X 3Y7; April 15, 2015
Amantadine hydrochloride Levodopa-induced dyskinesia Adamas Pharmaceuticals, Inc.;1900 Powell Street, Suite 750;Emeryville, California, 94608 April 9, 2015
Sodium ascorbate and menadione sodium bisulfite Noninfected painful total joint without mechanical complication IC-MedTech Corporation;9902 Indian Creek Lane;El Cajon, California, 92021 April 9, 2015
2-Pyrazinecarbonitrile, 5-[[5-2-(3-aminopropoxy)-6-methoxyphenyl]-1H-pyrazol-3-yl]amino] monomesylate monohydrate Anal cancer Eli Lilly and Company;Lilly Corporate Center;Indianapolis, Indiana, 46285 April 9, 2015
Modified human papillomavirus capsid protein conjugated to a near infrared dye Uveal melanoma Aura Biosciences, Inc.;85 Bolton Street;Cambridge, Massachusetts, 02140 April 8, 2015
Treosulfan Conditioning treatment prior to hematopoietic stem cell transplantation (HSCT) in malignant and non-malignant diseases in adults and pediatric patients Medac GmbH;TheaterstraBe 6, 22880 Wedel; April 8, 2015
Fluciclovine (18F)(anti-1-amino-3-fluorocyclobutane-1-carboxylic acid, labelled with Fluorine-18) Glioma Blue Earth Diagnostics Ltd.;215 Euston Rd, London, NW1 2BE; April 7, 2015
Eflornithine HCL Stomach Cancer Cancer Prevention Pharmaceuticals, Inc.;1760 East River Road, Suite 250;Tucson, Arizona, 85718 April 7, 2015
Human insulin (rDNA) Short bowel syndrome Nutrinia, Ltd.;15 Abba Hillel Silver Rd, 7th Floor, Ramat-Gan 5252208; April 6, 2015
Doxorubicin Cutaneous T-cell lymphoma Louis D. Falo, Jr.;University of Pittsburgh, Dep. of Dermatology, 3500 Fifth Avenue;Pittsburgh, Pennsylvania, 15213 April 6, 2015
Golimumab Polyarticular juvenile idiopathic arthritis in patients 0 through 18 years of age Janssen Research & Development, LLC;1400 McKean Road;Spring House, Pennsylvania, 19477 April 2, 2015
Bulevertide Hepatitis D MYR GmbH;Weinbergsweg 66, 61348 Bad Homburg; March 31, 2015
C21H27O10P Stomach Cancer Minneamrita Therapeutics, LLC;6 Hickory Court;Rock Island, Illinois, 61201 March 30, 2015
Roneparstat Multiple myeloma Leadiant Biosciences, Inc.;Via Motta 2, CH-6850 Mendrisio; March 19, 2015