Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Country Product Indication Sponsor Date
Trisaccharides A and B For use in ABO-incompatible solid organ transplantation, including kidney, heart, liver and pancreas Chembiomed, Ltd.;P.O. Box 8050, T6H 4NP; April 20, 1987
Trisaccharides A and B Moderate to severe clinical forms of hemolytic disease of the newborn arising from placental transfer of antibodies against blood group substances A and B Chembiomed, Ltd.;P.O. Box 8050, T6H 4NP; April 12, 1987
Surfactant (human) (amniotic fluid derived) Prevention and treatment of neonatal respiratory distress syndrome Merritt, T. Allen M.D.;2516 Stockton Boulevard;Sacramento, California, 95817 March 25, 1987
Somatropin For use in the long-term treatment of children who have growth failure due to a lack of adequate endogenous growth hormone secretion Genentech, Inc.;1 DNA Way;South San Francisco, California, 94080 March 6, 1987
Somatropin (rDNA origin) Growth hormone deficiency EMD Serono, Inc.;One Technology Place;Roackland, Massachusetts, 02370 March 6, 1987
Anti-tap-72 immunotoxin Metastatic colorectal adenocarcinoma Xoma Corporation;2910 Seventh Street;Berkeley, California, 94710 March 6, 1987
24,25 dihydroxycholecalciferol Uremic osteodystrophy Lemmon Company;1510 Delp Drive;Kulpsville, Pennsylvania, 19443 February 27, 1987
Calcitonin-human for injection Paget disease Novartis Pharmaceutical Corporation;59 Route 10;East Hanover, New Jersey, 07936 January 20, 1987
Ifosfamide Testicular cancer Bristol-Myers Squibb Pharmaceutical Research Institute;5 Research Parkway, P.O. Box 5100;Wallingford, Connecticut, 06492 January 20, 1987
Teriparatide Hypoparathyroidism Rhone-Poulenc Rorer Pharmaceuticals, Inc.;500 Arcola Road;Collegeville, Pennsylvania, 19426 January 9, 1987
Leucovorin For use in combination with 5-fluorouracil for the treatment of metastatic colorectal cancer Immunex Corporation;51 University Street;Seattle, Washington, 98101 December 8, 1986
Mazindol Duchenne muscular dystrophy Collipp, Platon J. M.D.;176 Memorial Dr.;Jesup, Georgia, 31545 December 8, 1986
Levocarnitine Manifestations of carnitine deficiency in patients with end stage renal disease who require dialysis Leadiant Biosciences, Inc.;9841 Washingtonian Blvd, Suite 500;Gaithersburg, Maryland, 20878 November 24, 1986
Nebacumab Patients with gram-negative bacteremia which has progressed to endotoxin shock Centocor, Inc.;244 Great Valley Parkway;Malvern, Pennsylvania, 19355 October 1, 1986
Interferon alfa-nl AIDS related Kaposi's sarcoma Burroughs Wellcome Company;3030 Cornwallis Road, P.O. Box 12700;Research Triangle Pk, North Carolina, 27709 August 25, 1986
Botulinum toxin type A Cervical dystonia Allergan, Inc.;2525 Dupont Drive, P.O. Box 19534;Irvine, California, 92623 August 20, 1986
Chlorhexidine gluconate mouthrinse For use in the amelioration of oral mucositis associated with cytoreductive therapy used in conditioning patients for bone marrow transplantation therapy Procter & Gamble Company;Sharon Wood Technical Center, 11370 Reed Hartman Highway;Cincinnati, Ohio, 45241 August 18, 1986
Erwinia L-asparaginase Acute lymphoblastic leukemia Jazz Pharmaceuticals, Inc.;3180 Porter Drive;Palo Alto, California, 94304 July 30, 1986
Anagrelide Thrombocytosis in chronic myelogenous leukemia Roberts Pharmaceutical Corp.;Meridian Center II, Four Industrial Way West;Eatontown, New Jersey, 07724 July 14, 1986
Disodium silibinin dihemisuccinate Hepatic intoxication by Amanita phalloides (mushroom poisoning) Pharmaquest Corporation;4470 Redwood Highway;San Rafael, California, 94903 July 10, 1986
Somatropin for injection For the long-term treatment of children who have growth failure due to inadequate secretion of normal endogenous growth hormone Eli Lilly and Company;Lilly Corporate Center;Indianapolis, Indiana, 46285 June 12, 1986
Sodium tetradecyl sulfate Bleeding esophageal varices Elkins-Sinn, Inc.;2 Esterbrook Lane;Cherry Hill, New Jersey, 08003 June 10, 1986
Dimethyl sulfoxide Cutaneous manifestations of scleroderma Research Industries Corp.;; June 6, 1986
Trimetrexate glucuronate Pneumocystis carinii pneumonia in AIDS patients Medimmune Oncology, Inc.;One Tower Bridge, 100 Front St., Suite 400;West Conshohocken, Pennsylvania, 19428 May 15, 1986
Monoclonal antibodies (murine or human) to B-cell lymphoma small lymphocytic lymphoma IDEC Pharmaceuticals Corporation;11011 Torreyana Road;San Diego, California, 92121 May 6, 1986