Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

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Country Product Indication Sponsor Date
Digitoxin Soft tissue sarcomas SimRx Advisors LLC;247 West 87th Street, Suite 7G;New York, New York, 10024 October 18, 2001
(R)-N-[2-(6-chloro-5-methoxy-1H-indol-3-yl)propyl]acetamide Circadian rhythm sleep disorders in blind people with no light perception Phase 2 Discovery, Inc.;3130 Highland Avenue, Third Floor;Cincinnati, Ohio, 45219 October 3, 2001
DHA-paclitaxel Pancreatic Cancer Luitpold Pharmaceuticals, Inc.;One Luitpold Drive;Shirley, New York, 11976 September 25, 2001
Recombinant human acid sphingomyelinase Niemann-Pick disease Genzyme Europe B.V. September 19, 2001
Beclomethasone 17,21-dipropionate Graft Versus Host Disease Soligenix, Inc.;29 Emmons Drive;Princeton, New Jersey, 08540 August 28, 2001
Recombinant human endostatin protein Neuroendocrine tumors EntreMed, Inc.;9640 Medical Center Drive;Rockville, Maryland, 20850 August 13, 2001
Benzophenone-3, octylmethoxycinnamate, avobenzone, titanium dioxide, zinc oxide For the prevention of visible light induced skin photosensitivity as a result of porfimer sodium photodynamic therapy Fallien Cosmeceuticals Ltd.;677 W. Dekalb Pike;King of Prussia, Pennsylvania, 19406 August 13, 2001
Imexon Metastatic Melanoma AmpliMed Corporation;2321 Camino La Zorrela;Tucson, Arizona, 85718 August 3, 2001
Angiotensin 1-7 Myelodysplastic syndrome Tarix Pharmaceuticals, Ltd;12 Bow Street;Cambridge, Massachusetts, 02138 August 3, 2001
2-chloroethyl-3-sarcosinamide-1-nitrosourea Treatment for malignant gliomas Lawrence Panasci, MD;Professor of Medicine, McGill University, 3755 Cote Ste Catherine; August 3, 2001
Thyrotropin alfa Well-differentiated papillary, follicular or combined papillary/follicular carcinomas of the thyroid Genzyme Corporation;One Kendall Square;Cambridge, Massachusetts, 02139 August 3, 2001
L-glutamine Sickle cell anemia Emmaus Medical, Inc.;21250 Hawthorne Blvd., Suite 800;Torrance, California, 90503 August 1, 2001
Intraoral fluoride releasing system Squamous cell carcinoma of head and neck Digestive Care, Inc.;1120 Win Drive;Bethlehem, Pennsylvania, 18017 July 31, 2001
2-methoxyestradiol Multiple myeloma EntreMed, Inc.;Research Triangle Park Center, Suite 400;Durham, North Carolina, 27703 July 10, 2001
Reviparin sodium Long-term treatment of acute deep vein trombosis with or without pulmonary embolism in pregnant patients Abbott;Abbott Laboratories, Dept. 389, Bldg. J-45, 200 Abbott Park Rd.;Abbott Park, Illinois, 60064 June 18, 2001
Reviparin sodium Deep vein thrombosis which may lead to pulmonary embolism in pediatric patients Abbott;Abbott Laboratories, Dept. 389, Bldg. J-45, 200 Abbott Park Rd.;Abbott Park, Illinois, 60064 June 18, 2001
Latrodectus immune F(ab)2 Black widow spider envenomations Instituto Bioclon, S.A. de C.V.;Tlalpan,, No. 4687 Colonia Toriello Guerra;Tlalpan June 18, 2001
Adeno-associated viral vector containing the gene for human coagulation factor IX Intramuscular treatment of patients with moderate to severe hemophilia Avigen, Inc.;1301 Harbor Bay Parkway;Alameda, California, 94502 June 13, 2001
Adeno-associated viral vector containing the gene for human coagulation factor IX Intrahepatic treatment of patients with moderate to severe hemophilia Avigen, Inc.;1301 Harbor Bay Parkway;Alameda, California, 94502 June 13, 2001
Staphylococcal immunoglobulin (human) Reduction (prevention) of nosocomial bacteremia caused by staphylococci in very low birth weight infants Inhibitex, Inc.;8995 Westside Parkway, Suite 150;Alpharetta, Georgia, 30004 June 13, 2001
Glatiramer acetate for injection Primary-progressive multiple sclerosis Teva Pharmaceuticals USA;1090 Horsham Road;North Wales, Pennsylvania, 19454 June 5, 2001
9-nitro-20-(S)-camptothecin Pediatric HIV infection/AIDS NovoMed Pharmaceuticals, Inc.;P.O. Box 900;Germantown, Maryland, 20875 May 15, 2001
Perflubron Acute respiratory distress syndrome PFC Development/New Alliance Pharmaceutical;15021 Venture Blvd;Sherman Oaks, California, 91403 April 26, 2001
Interferon-alfa-1b Multiple myeloma Ernest C.Borden;Center for Cancer Drud Discovery and Development, 9500 Euclid Avenue;Clevland, Ohio, 44195 April 17, 2001
Recombinant human highly phosphorylated alpha-L-iduronidase (rhHP-IDUA) Enzyme replacement therapy in patients with all subtypes of Mucopolysaccharidosis I Novazyme Pharmaceuticals, Inc.;800 Research Parkway, Suite 200;Oklahoma City, Oklahoma, 73104 April 11, 2001