Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Country Product Indication Sponsor Date
Albuterol Prevention of paralysis due to spinal cord injury MotoGen, Inc.;3 Pine View Road;Mount Kisco, New York, 10549 March 12, 2002
Aztreonam Cystic fibrosis Gilead Sciences (formerly Corus Pharma);199 East Blaine St;Seattle, Washington, 98102 March 12, 2002
I(131)-TM-601 (chlorotoxin) Glioma Morphotek, Inc.;210 Welsh Pool Road;Exon, Pennsylvania, 19341 February 14, 2002
Creatine Amyotrophic lateral sclerosis Avicena Group, Inc.;580 California St., Suite 1600;San Francisco, California, 94104 February 12, 2002
Recombinant immunotoxin combining the functional components of antibody against mesothelin and the enzymatic activity of a pseudomonas exotoxin Ovarian epithelial cancer National Institutes of Health;Cancer Therapy Evaluation Program, 6130 Executive Blvd, Suite 7111;Rockville, Maryland, 20852 February 11, 2002
Bioartificial liver system utilizing xenogenic hepatocytes in a hollow fiber bioreactor cartridge (BAL) Patients with acute liver failure presenting with encephalopathy deteriorating beyond Parson's grade 2 Excorp Medical, Inc.;Suite 235, 7200 Hudson Blvd.;Oakdale, Minnesota, 55128 February 11, 2002
Recombinant immunotoxin combining the functional components of antibody against mesothelin and the enzymatic activity of a pseudomonas exotoxin Malignant pleural mesothelioma National Institutes of Health;Cancer Therapy Evaluation Program, 6130 Executive Blvd, Suite 7111;Rockville, Maryland, 20852 February 11, 2002
Clofarabine Acute lymphoblastic leukemia Genzyme Corporation;4545 Horizon Hill Blvd.;San Antonio, Texas, 78229 February 7, 2002
Adenovirus-mediated Herpes simplex Virus-thymidine kinase gene Glioma Gliotherapy Limited February 6, 2002
Lipase, amylase, and protease Pancreatic insufficiency Altus Biologics Inc.;625 Putnam Avenue;Cambridge, Massachusetts, 02139 January 23, 2002
Carbamic acid, [[4-[[3-[[4-[1-(4-hydroxyphenyl)-1-methyl-ethyl]phenoxy]methyl]phenyl]methoxy]-phenyl]iminomethyl]-,ethyl ester Cystic fibrosis Boehringer Ingelheim Pharmaceuticals, Inc;900 Ridgebury Road, P.O. Box 368;Ridgefield, Connecticut, 06877 January 15, 2002
Deferiprone Iron overload in patients with hematologic disorders requiring chronic transfusion therapy ApoPharma, Inc. A Division of;Apotex Research Inc., Toronto, Canada M9L 1T9; December 12, 2001
Bryostatin-1 Esophageal cancer GPC Biotech, Inc.;610 Lincoln Street;Waltham, Massachusetts, 02451 December 3, 2001
Conjugate of human transferrin and a mutant diphtheria toxin (CRM 107) Malignant tumors of the central nervous system Xenova Biomedix Limited;957 Budkingham Avenue, Slough; December 3, 2001
Azacitidine Myelodysplastic syndromes Celgene Corporation;9900 W. 109th Street, Suite 300;Overland Park, Kansas, 66210 December 3, 2001
Hu1D10, humanized monoclonal antibody For use in the treatment of 1D10+ B cell non-Hodgkin's lymphoma PDL BioPharma, Inc.;34801 Campus Drive;Fremont, California, 94555 November 28, 2001
2-chloroethyl-3-sarcosinamide-1-nitrosourea Glioma Pangene Corporation;5500 Stewart Avenue;Fremont, California, 94538 November 15, 2001
Cintredekin besudotox Glioma Insys Development Company, Inc.;1333 South Sprectum Blvd, Suite 100;Chandler, Arizona, 85286 November 2, 2001
Digitoxin Ovarian cancer SimRx Advisors LLC;247 West 87th Street, Suite 7G;New York, New York, 10024 November 2, 2001
IL13-PE38QQR Glioma Insys Development Company, Inc.;1333 South Sprectum Blvd, Suite 100;Chandler, Arizona, 85286 November 2, 2001
Arsenic Acute myelocytic leukemia Teva Branded Pharmaceutical Products R&D;, Inc.;41 Moores Road, P. O. Box 4011;Frazer, Pennsylvania, 19355 November 2, 2001
T-cell depleted stem cell enriched cellular product from peripheal b lood stem cells Chronic granulomatous disease Nexell Therapeutics Inc.;9 Parker;Irvine, California, 92618 November 1, 2001
Acetylcysteine For the intravenous treatment of moderate to severe acetaminophen overdose Cumberland Pharmaceuticals, Inc.;209 10th Street South, Suite 332;Nashville, Tennessee, 37203 October 19, 2001
Nitisinone Alkaptonuria Swedish Orphan AB;Kungsgatan 37, 7th Floor, SE-111 56; October 19, 2001
Digitoxin Soft tissue sarcomas SimRx Advisors LLC;247 West 87th Street, Suite 7G;New York, New York, 10024 October 18, 2001