Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Country Product Indication Sponsor Date
Recombinant urate oxidase Prophylaxis of chemotherapy-induced hyperuricemia Sanofi-Synthelabo Research;9 Great Valley Parkway;Malvern, Pennsylvania, 19355 October 11, 2000
Bosentan Pulmonary Arterial Hypertension Actelion Pharmaceuticals, Ltd.;1840 Gateway Drive, Suite 300;Cherry Hill, New Jersey, 08002 October 6, 2000
Bosentan Pulmonary arterial hypertension Actelion Pharmaceuticals, Ltd.;1840 Gateway Drive, Suite 300;Cherry Hill, New Jersey, 08002 October 6, 2000
Bosentan Pulmonary arterial hypertension Actelion Life Sciences Ltd.;1840 Gateway Dr., 2nd Floor;San Mateo, California, 94404 October 6, 2000
Eculizumab Dermatomyositis Alexion Pharmaceuticals, Inc.;352 Knotter Drive;Cheshire, Connecticut, 06410 September 21, 2000
DNP-Modified autologous tumor vaccine Ovarian cancer AVAX Technologies, Inc.;9200 Indian Creek Parkway, Building 9, Suite 200;Overland Park, Kansas, 66210 September 21, 2000
Recombinant human highly phosphorylated acid alpha-glucosidase Pompe disease Novazyme Pharmaceuticals, Inc.;800 Research Parkway, Suite 200;Oklahoma City, Oklahoma, 73104 September 20, 2000
3,5,3′-triiodothyroacetate Well-differentiated papillary, follicular or combined papillary/follicular carcinomas of the thyroid gland Elliot Danforth, Jr., M.D.;University of Vermont, 84 Beartown Road;Underhill, Vermont, 05489 September 20, 2000
Lanreotide Treatment for acromegly IPSEN, Inc.;27 Maple Street;Milford, Massachusetts, 01757 September 11, 2000
Cisplatin/epinephrine Metastatic malignant melanoma Matrix Pharmaceutical, Inc.;34700 Campus Drive;Fremont, California, 94555 September 7, 2000
Anti-thymocyte Globulin (rabbit) Myelodysplastic syndrome Genzyme Corporation;A Sanofi Company, 500 Kendall Street;Cambridge, Massachusetts, 02142 September 6, 2000
Calfactant Acute respiratory distress syndrome ONY, Inc.;Baird Research Park, Suite 114;Amherst, New York, 14228 September 5, 2000
Calfactant Acute respiratory distress syndrome ONY, Inc.;Baird Research Park, Suite 114;Amherst, NY, 14228 September 5, 2000
Zoledronate Tumor induced hypercalcemia Novartis Pharmaceuticals Corp.;59 Route 10;East Hanover, New Jersey, 07936 August 18, 2000
Natural human lymphoblastoid interferon-alpha Papillomavirus warts in the oral cavity of HIV positive patients Amarillo Biosciences, Inc.;4134 Business Park Drive;Amarillo, Texas, 79110 August 10, 2000
Trimetrexate Metastatic osteogenic sarcoma Medimmune Oncology, Inc.;One MedImmune Way;Gaithersburg, Maryland, 20878 August 10, 2000
Chimeric, humanized monoclonal antibody to staphylococcus Prophylaxis of Staphylococcus epidermidis sepsis in low birth weight (1500 grams or less) infants Biosynexus, Inc.;9298 Gaither Road;Rockville, Maryland, 20877 August 3, 2000
Hypericin Glioblastoma HyBiopharma, Inc.;2500 York Road, Suite 100;Jamison, Pennsylvania, 18929 August 3, 2000
Fluocinolone Treatment uveitis involving the posterior segment of the eye Bausch & Lomb Pharmaceuticals, Inc.;8500 Hidden River Parkway;Tampa, Florida, 33637 July 31, 2000
Abetimus Lupus nephritis La Jolla Pharmaceutical Co.;6455 Nancy Ridge Dr.;San Diego, California, 92121 July 28, 2000
Chimeric (human-murine) G250 IgG monoclonal antibody Renal cancer Wilex Biotechnology GmbH;Grillparzerstrasse 10B, 81675 Munich; July 24, 2000
Arsenic trioxide Myelodysplastic syndrome Teva Branded Pharmaceutical Products R&D;, Inc.;41 Moores Road, P.O. Box 4011;Frazer, Pennsylvania, 19355 July 17, 2000
Carmustine Intracranial malignancies Direct Therapeutics, Inc.;460 Seaport Court, Suite 220;Redwood, California, 94063 July 3, 2000
Cetuximab Squamous cell carcinoma of head and neck ImClone Systems Incorporated;33 ImClone Drive;Branchburg, New Jersey, 08876 July 3, 2000
Fluorouracil Glioblastoma Ethypharm SA;194 Bureaux de la Colline - Batiment D, 92213 Saint-Cloud Cedex; June 29, 2000