Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Country Product Indication Sponsor Date
Coagulation factor VIIa (recombinant) Hemophilia A Novo Nordisk, Inc.;100 College Road West;Princeton, New Jersey, 08540 June 18, 2004
Coagulation factor VIIa (recombinant) Prevention of bleeding episodes in Glanzmann's thrombasthenia Novo Nordisk, Inc.;100 College Road West;Princeton, New Jersey, 08540 June 18, 2004
Vaccinia Immune Globulin (Human) Intravenous Smallpox DynPort Vaccine Company LLC;64 Thomas Johnson Drive;Frederick, Maryland, 21702 June 18, 2004
Coagulation factor VIIa (recombinant) Bleeding episodes in Glanzmann's thrombasthenia Novo Nordisk Inc.;800 Scudders Mill Rd.;Plainsboro, New Jersey, 08536 June 18, 2004
Thymosin beta 4 Epidermolysis bullosa GtreeBNT Co., Ltd;22nd Fl, Parkview Tower, 248 Jungjail-ro, Bundang-gu;Gyeonggi-do May 28, 2004
Diethylnorspermine (DENSPM) Hepatocellular Carcinoma Genzyme Corporation;153 Second Avenue;Waltham, Massachusetts, 02451 May 25, 2004
Immune Globulin Intravenous (human) Treatment for Guillain Barre Syndrome ZLB Bioplasma AG;Wankdorfstrasse 10, CH-3000 Bern 22; May 4, 2004
Diethylenetriaminepentaacetic acid (DTPA) Patients with known or suspected internal contamination with plutonium, americium, or curium to increase the rates of elimination Hameln Pharmaceuticals gmbh;Langes Feld 13;Hameln April 28, 2004
Etaracizumab Metastatic Melanoma MedImmune, LLC;One MedImmune Way;Gaithersburg, Maryland, 20878 April 14, 2004
Diethylenetriaminepentaacetate (DPTA) For treatment of patients with known or suspected internal contamination with plutonium, americium or curium to increase the rates of elimination CIS-US;10 DeAngelo Drive;Bedford, Massachusetts, 01730 April 14, 2004
Deferitrin Iron overload Genzyme Corporation;153 Second Avenue;Waltham, Massachusetts, 02451 April 14, 2004
Fluoxetine Body dysmorphic disorder in children and adolescents Hollander, Eric MD;The Mount Sinai School of Medicine, One Gustave L. Levy Place;New York, New York, 10029 April 14, 2004
Ubiquinol, coenzyme Q10, ubiquinone Pediatric congestive heart failure Gel-Tec, Division of Tishcon Corporation;30 New York Avenue, P. O. Box 331;Westbury, New York, 11590 April 12, 2004
Hydralazine Severe intrapartum hypertension (diastolic blood pressure greater than or equal to 110 or systolic blood pressure greater than or equal to 160) associated with severe preeclampsia/eclampsia of pregnancy Bioniche Pharma USA LLC;272 E. Deerpath Road, Suite 304;Lake Forest, Illinois, 60045 April 9, 2004
Vapreotide Symptomatic carcinoid tumors H3 Pharma, Inc.;666 Sherbrooke Street West Suite 1400, Montreal, Quebec,; April 6, 2004
Dexrazoxane Anthracycline extravasation during chemotherapy Clinigen Healthcare Ltd.;Pitcairn House, First Avenue, Burton on Trent;Staffordshire March 25, 2004
Sodium thiosulfate Prevention of platinum-induced ototoxicity in pediatric patients Fennec Pharmaceuticals, Inc.;PO Box 13628, 68 T.W. Alexander Drive;Research Triangle Park, North Carolina, 27709 March 17, 2004
Alpha-1-acid glycoprotein Tricyclic antidepressant poisoning Bio Products Laboratory;Dagger Lane, Elstree, Hertfordshire, WD6 3BX; March 17, 2004
Immune Globulin (Human) containing high titers of West Nile virus antibodies West Nile virus OMRIX Biopharmaceuticals, Ltd.;Plasma Fractionation Institute, Ramat Gan 52621; March 17, 2004
Antihemophilic factor (recombinant), porcine sequence Treatment and prevention of episodic bleeding in patients with inhibitor antibodies to human coagulation factor VIII Baxalta US, Inc.;1 Baxter Way, Mail Box Number 1A-3;Westlake Village, California, 91362 March 16, 2004
Somatropin Patients with HIV-associated adipose redistribution syndrome EMD Serono, Inc.;One Technology Place;Rockland, Massachusetts, 02370 March 16, 2004
3-(4’aminoisoindoline-1′-one)-1-piperidine-2,6-dione Myelodysplastic syndromes Celgene Europe Limited March 8, 2004
Alpha-1-acid glycoprotein Cocaine overdose Bio Products Laboratory;Dagger Lane, Elstree, Hertfordshire, WD6 3BX; March 5, 2004
DEAE-rebeccamycin Bile duct tumors Helsinn Healthcare SA;Via Pian Scairolo, 6912 Pazzallo, Lugano; March 1, 2004
Trisodium zinc Diethylenetriaminepentaacetate Patients with known or suspected internal contamination with plutonium, americium, or curium to increase the rate of elimination CustomCare Pharmacy;5710 Hoover Blvd;Tampa, Florida, 33634 February 27, 2004