Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Country Product Indication Sponsor Date
5,5′,5″-[Phosphinothioylidyne-tris(imino-2,1-ethanediyl)]tris[5-methylchelidoninium]trihydroide hexahydrochloride Pancreatic Cancer Now Pharm AG;241, route d'Arlon, L-1150; August 20, 2003
Eculizumab Hemoglobinuria Alexion Pharmaceuticals, Inc.;352 Knotter Drive;Cheshire, Connecticut, 06410 August 20, 2003
Debrase Debridement of acute, deep dermal burns in hospitalized patients MediWound, Ltd.;42 Hayarkon Street, Industrial Zone; August 20, 2003
(3S)-3-[(2S)-2-({N-[2-tert-butyl)phenyl]carbamoyl}carbonylamino) propanoylamino]-4-oxo-5-(2,3,5,6-tetrafluorophenoxy) pentanoci acid Patients undergoing solid organ transplantation Pfizer Global Research and Development;50 Pequot Avenue;New London, Connecticut, 06320 August 19, 2003
Dehydroepiandrosterone (DHEA) Replacement therapy in individuals with adrenal insufficiency Paladin Labs, Inc.;6111 Royalmount Avenue, Suite 102, Montreal;Quebec H4P 2T4 August 19, 2003
Cultured, partially T-Cell depleted, allogenic thymic tissue for transplantation DiGeorge syndrome Enzyvant Therapeutics GmbH;Viaduktstrasse 8, CH-4051 Basel; August 15, 2003
2-0-Butyryl-1-0-octyl-myo-inositol 3,4,5,6-tetrakisphosphate Cystic fibrosis Inologic, Inc.;101 Elliott Ave., West;Seattle, Washington, 98119 August 15, 2003
Mx-dnG1 or Rexin-G retroviral vector Pancreatic Cancer Epeius Biotechnologies Corporation;345 Pioneer Drive, 1803W;Glendale, California, 91203 August 15, 2003
Combretastatin A4 Phosphate Medullary thyroid cancer Mateon Therapeutics, Inc.;701 Gateway Boulevard, Suite 210;South San Francisco, California, 94080 July 23, 2003
Erlotinib Hydrochloride Malignant gliomas Genentech, Inc;1 DNA Way;South San Francisco, California, 94080 July 18, 2003
Cholic acid (3 alpha, 7 alpha, 12 alpha trihydroxy 5-beta cholanolic acid) Bile Acid Synthesis Asklepion Pharmaceuticals, LLC;729 East Pratt Street, Suite 360;Baltimore, MD, 21202 July 18, 2003
Chimeric monoclonal antibody to CD30 (anti-CD30 antibody) Hodgkin’s disease Seattle Genetics, Inc;21823 30th Drive, Southeast;Bothell, Washington, 98021 July 18, 2003
Conjugated bile acids Short bowel syndrome Jarrow Formulas, Inc.;1824 S. Robertson Blvd.;Los Angeles, California, 90035 July 18, 2003
Dual antibody including HBV-Ab 17, libivirumab, and HBV-Ab 19, exbivirumab For the prevention of hepatitis B virus (HBV) reinfection in patients who have received a liver transplantation Cubist Pharmaceuticals;65 Hayden Avenue;Lexington, Massachusetts, 02421 July 15, 2003
(R)-N-[2-(6-Chloro-methoxy-1H-indol-3yl)propyl]acetamide Tardive dyskinesia Phase 2 Discovery, Inc.;3130 Highland Ave., Third Floor;Cincinnati, Ohio, 45219 July 3, 2003
Ferric hexacyanoferrate (II) “Prussian Blue” Patients with known or suspected internal contamination with radioactive or non-radioactive cesium or thallium Degussa AG;Weissfrauenstr.9, D-60287;Frankfurt June 26, 2003
Arsenic trioxide Hepatocellular Carcinoma Teva Branded Pharmaceutical Products R&D;, Inc.;41 Moores Road, P. O. Box 4011;Frazer, Pennsylvania, 19355 June 13, 2003
Diphenylcyclopenone Alopecia areata Lloyd E. King, Jr.;1900 Patterson Street, Suite 104;Nashville, Tennessee, 37203 June 13, 2003
Diferuloylmethane Cystic fibrosis Allertein Therapeutics, LLC;640 Sasco Hill Road;Fairfield, Connecticut, 06824 June 13, 2003
Protaxel Ovarian cancer Biophysica, Inc.;2159 Avenida de la Playa, Suite B;La Jolla, California, 92037 May 21, 2003
Factor XIII [A2] homodimer, recombinant DNA origin Congenital FXIII deficiency Novo Nordisk Pharmaceuticals, INc.;100 College Road West;Princeton, New Jersey, 08540 May 21, 2003
Defibrotide Hepatic venoocclusive disease Jazz Pharmaceuticals, Inc.;3180 Porter Dr.;Palo Alto, California, 94304 May 21, 2003
Infliximab Sarcoidosis Centocor, Inc.;200 Great Valley Parkway;Malvern, Pennsylvania, 19355 May 21, 2003
Anti-CEA Sheep-human chimeric monoclonal antibody labeled w/iodine-131 (KAb201) Pancreatic Cancer Avaant Pharmaceuticals India Ltd.;3rd Floor, Neelkanth Commercial Centre, Mumbai - 400 099; May 21, 2003
Arsenic trioxide Chronic lymphocytic leukemia Teva Branded Pharmaceutical Products R&D;, Inc.;41 Moores Road, P.O. Box 4011;Frazer, Pennsylvania, 19355 May 13, 2003