Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Country Product Indication Sponsor Date
Implitapide Patients with Fredrickson type I or V hyperlipoproteinemia Medical Research Laboratories International;2 Tesseneer Drive;Highland Heights, Kentucky, 41076 August 19, 2004
Iloprost inhalation solution Pulmonary Arterial Hypertension CoTherix, Inc.;5000 Shoreline Court;South San Francisco, California, 94080 August 17, 2004
Nucleic acid aptamer binding to tumor cell nucleolin Pancreatic Cancer Antisoma Research Ltd.;Hanger Lane, London; August 17, 2004
(6R,S)5,10-methylene-tetrahydrofolic acid Pancreatic Cancer Adventrx Pharmaceuticals, Inc.;6725 Mesa Ridge Road, Suite 100;San Diego, California, 92121 August 13, 2004
(1S)-1-(9-deazahypoxanthin-9-yl)-1,4-dideoxy-1,4-imino-D-ribitol-hydrochloride Acute lymphoblastic leukemia Mundipharma Research Limited;Cambridge Science Park, Cambridge CB4 0GW;England August 13, 2004
N-[4-(4-amino-2-ethyl-1H-imidazo[4,5-c]quinolin-1-yl)butyl]methanesulfonamide Stages IIB-IV melanoma Pfizer, Inc.;50 Pequot, 6025-A3106;New London, Connecticut, 06320 August 13, 2004
Dacetuzumab Multiple myeloma Seattle Genetics, Inc.;21823 30th Drive Southeast;Bothell, Washington, 98021 August 13, 2004
Implitapide Homozygous Familial Hypercholesterolemia Medical Research Laboratories International;2 Tesseneer Drive;Highland Heights, Kentucky, 41076 August 13, 2004
Dexanabinol For the attenuation or amelioration of the long-term neurological sequelae associated with moderate and severe traumatic brain injury Pharmos Corporation;99 Wood Avenue, Suite 311;Iselin, New Jersey, 08830 August 11, 2004
(1S)-1-(9-deazahypoxanthin-9-yl)-1,4-dideoxy-1,4-imino-D-ribitol-hydrochloride Hairy cell leukemia Mundipharma Research Ltd.;Cambridge Science Park, Cambridge CB4 0GW; August 10, 2004
Ciclosporin (inhalation use) Bronchiolitis obliterans syndrome Breath Therapeutics GmbH July 29, 2004
Efaproxiral Adjunct to whole brain radiation therapy for the treatment of brain metastases in patients with breast cancer Allos Therapeutics, Inc.;11080 CirclePoint Road, Suite 200;Westminster, Colorado, 80020 July 28, 2004
Multi-ligand somatostatin analog VIPoma Novartis Pharmaceuticals Corporation;One Health Plaza;East Hanover, New Jersey, 07936 July 27, 2004
Immune Globulin (Human) Chronic inflammatory demyelinating polyneuropathy Grifols Therapeutics, Inc.;8368 US 70 Business Hwy West;Clayton, North Carolina, 27520 July 27, 2004
Coagulation factor VIIa (recombinant) Prevention of bleeding episodes in patients with acquired inhibitors to Factor VIII or Factor IX Novo Nordisk, Inc.;100 College Road West;Princeton, New Jersey, 08540 July 21, 2004
Posaconazole Mucormycosis Schering-Plough Corporation;2000 Galloping Hill Road;Kenilwortoh, New Jersey, 07033 July 16, 2004
Doripenem Cystic fibrosis Shionogi, Inc.;300 Campus Drive, Suite 300;Florham Park, New Jersey, 07932 July 16, 2004
Immortalized human liver cells found in the extracorporeal liver assist device Fulminant hepatic failure (acute liver failure) Vital Therapies, Inc.;15222 Avenue of Science, Suite C;San Diego, California, 92128 July 16, 2004
C1 esterase inhibitor (human) Angioedema Shire;300 Shire Way;Lexington, Massachusetts, 02421 July 16, 2004
Coagulation Factor VIIa (Recombinant) Bleeding episodes in patients with acquired inhibitors to Factor VIII or Factor IX Novo Nordisk, Inc.;100 College Road West;Princeton, New Jersey, 08540 July 16, 2004
Ambrisentan Pulmonary Arterial Hypertension Gilead Colorado;7575 West 103rd Avenue, Suite 102;Westminister, Colorado, 80021 July 16, 2004
Melatonin Non-24-hour Sleep Wake Disorder Neurim Pharmaceuticals, Ltd.;8 Hanechoshet St.;Tel-Aviv July 9, 2004
Tipifarnib Acute myeloid leukemia Johnson & Johnson Pharmaceutical Research & Dev.;920 U.S. Highway 202;Raritan, New Jersey, 08869 July 6, 2004
Vaccinia Immune Globulin (Human) Intravenous Complications of vaccinia vaccination Cangene Corporation;104 Chancellor Matheson Road;Winnipeg, ManitobaR3T 5Y3 June 18, 2004
Plitidepsin Acute lymphoblastic leukemia PharmaMar USA, Inc;University Park at M.I.T., Sidney Street;Cambridge, Massachusetts, 02139 June 18, 2004