Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

Become a Partner.

Country Product Indication Sponsor Date
Mifepristone Cushing’s syndrome HRA Pharma;15 , rue Beranger, 75003 Paris; February 7, 2005
Tramadol hydrochloride Painful HIV-associated neuropathy TheraQuest Biosciences, LLC;146 Medinah Drive;Blue Bell, Pennsylvania, 19422 January 28, 2005
Allogeneic T-cells cultured with anti-CD3 and IL-2; transduced with retroviral vector (SFCMM-3), expressing herpes simplex 1 virus-thymidine kinase (HSV-TK) and truncated low affinity nerve growth factor receptor; selected with anti-low affinity nerve gro Immunotherapy for acceleration of T-cell reconstitution in patients undergoing allogeneic hematopoietic stem cell transplantation MolMed S.p.A.;Via Olgettina 58;Milan January 28, 2005
Deferoxamine starch conjugate Acute iron poisoning Biomedical Frontiers, Inc.;1087 10th Avenue, SE;Minneapolis, Minnesota, 55414 January 28, 2005
N-(2,3-dihydro-3,3-dimethyl-1H-indol-6-yl)-2-[(4-pyridinylmethyl)amino]-3-pyridinecarboxamide, phosphate (1:2) Gastrointestinal Stromal Tumors Amgen, Inc.;One Amgen Center Drive;Thousand Oaks, California, 91320 January 13, 2005
Bedaquiline; (1R,2S) 6-bromo-alpha-[2-(dimethylamino)ethyl]-2-methoxy-alpha-(1-naphthyl)-beta-phenyl-3-quinolineethanol Active tuberculosis Janssen Research & Development, LLC;920 Route 202 South;Raritan, New Jersey, 08869 January 10, 2005
Ataluren Muscular Dystrophy resulting from premature stop mutations in the dystrohin gene PTC Therapeutics, Inc.;100 Corporate Court;South Plainfield, New Jersey, 07080 January 10, 2005
(2Z)-2-cyano-3-3hydroxy-N-[4-(trifluoromethly)phenyl]-2-hepten-6-ynamide Prevention of acute rejection following kidney, heart, and liver transplantation Astellas Pharma US, Inc.;Three Parkway North;Deerfield, Illinois, 60015 January 10, 2005
Doxorubicin HCL liposome injection Multiple myeloma Johnson & Johnson Pharmaceutical Research & Dev.;920 US Highway 202, P. O. Box 300;Raritan, 08869 December 29, 2004
Floxuridine, FUDR Intraperitoneal treatment of gastric cancer Franco Muggia, M.D.;160 East 34th Street;New York, New York, 10016 December 22, 2004
Alpha1-Proteinase Inhibitor (Human) Inhalation therapy for the treatment of congential deficiency of alpha1-proteinase inhibitor Kamada Ltd.;7 Sapir Street;Ness Ziona December 22, 2004
Rilonacept CIAS1-Associated Periodic Syndromes Regeneron Pharmaceuticals, Inc.;777 Old Saw Mill River Road;Tarrytown, New York, 10591 December 20, 2004
Temsirolimus Renal cancer Wyeth Pharmaceuticals, Inc.;P. O. Box 8299;Philadelphia, Pennsylvania, 19101 December 16, 2004
20-mer complementary to Akt mRNA Stomach Cancer Rexahn Corporation;9620 Medical Center Drive;Rockville, Maryland, 20850 December 10, 2004
(9-[N-(3-morpholinopropyl)-sulfonyl]-5,6-dihydro-5-oxo-11-H-indeno [1,2-c] isoquinoline methanesulfonic acid Prevention of post-operative complications of aortic anuerysm surgical repair Inotek Pharmaceuticals Corporation;100 Cummings Center;Beverly, Massachusetts, 01915 December 8, 2004
20-mer oligonucleotide complementary to Akt mRNA Pancreatic Cancer Rexahn Corporation;9620 Medical Center Drive;Rockville, Maryland, 20850 December 8, 2004
20-mer oligonucleotide complementary to Akt mRNA Glioblastoma Rexahn Corporation;9620 Medical Center Drive;Rockville, Maryland, 20850 December 8, 2004
20-mer oligonucleotide complementary to Akt mRNA Renal cancer Rexahn Corporation;9620 Medical Center Drive;Rockville, Maryland, 20850 December 1, 2004
20-mer oligonucleotide complementary to Akt mRNA Ovarian cancer Rexahn Corporation;9620 Medical Center Drive;Rockville, Maryland, 20850 December 1, 2004
Porfimer sodium Bile duct cancer Concordia Laboratories, Inc.;Canewood Business Centre, St. Michael, Barbados BB; November 18, 2004
Potassium Iodide Oral Solution For use as a thyroid blocking agent in pediatric patients exposed to radiactive iodine Fleming & Company, Pharmaceuticals;1733 Gilsinn Lane;Fenton, Missouri, 63026 November 17, 2004
Nimotuzumab Glioma InnoKeys PTE Ltd.;26 Bukit Batok East Avenue 2 #03-10; November 17, 2004
Sitaxsentan Sodium Pulmonary Arterial Hypertension Pfizer Global Research and Development;50 Pequot Avenue 6025-B4137;New London, Connecticut, 06320 November 2, 2004
Human monoclonal antibody against platelet-derived growth factor D IgA Nephropathy CuraGen Corporation;322 East Main Street;Branford, Connecticut, 06405 November 2, 2004
Cyclosporin A Amyotrophic lateral sclerosis Maas Biolab,LLC;Tecnology Ventures Corporation Technopolis, 1155 University Blvd., SE;Albuquerque, New Mexico, 87106 October 29, 2004