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non-replicating recombinant adeno-associated virus (AAV) vector of serotype 9 expressing human iduronate-2-sulfatase |
|---|---|
| Trade Name | |
| Orphan Indication | Hunter Syndrome |
| USA Market Approval | USA |
| USA Designation Date | 2015-12-08 00:00:00 |
| Sponsor | REGENXBIO, Inc.;9712 Medical Center Drive, Suite 100;Rockville, Maryland, 20850 |
