adeno-associated virus serotype 9 vector containing human Iduronate-2-sulfatase transgene

adeno-associated virus serotype 9 vector containing human Iduronate-2-sulfatase transgene
Trade Name
Orphan Indication Hunter Syndrome
USA Market Approval USA
USA Designation Date 2015-07-16 00:00:00
Sponsor Laboratorios del Dr. Esteve, S.A.;Av. Marie de Deu de Montserrat, 221;Barcelona