Adeno-associated viral vector serotype 8 encoding engineered rhodopsin DNA-binding repressor and human rhodopsin expression cassettes

Adeno-associated viral vector serotype 8 encoding engineered rhodopsin DNA-binding repressor and human rhodopsin expression cassettes
Trade Name
Orphan Indication Retinitis pigmentosa
EU Market Approval EU
EU Designation Date 2016-12-12 00:00:00
Sponsor Fondazione Telethon