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  5. Antisense oligonucleotide targeting theUSH2Agene

Antisense oligonucleotide targeting theUSH2Agene

April 13, 2017
Antisense oligonucleotide targeting theUSH2Agene
Trade Name
Orphan Indication Retinitis pigmentosa
EU Market Approval EU
EU Designation Date 2017-03-20 00:00:00
Sponsor ProQR Therapeutics IV BV
Related Access Program
Rigel Pharmaceuticals – Immune Thrombocytopenic Purpura

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More Treatment
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