|
adeno-associated virus serotype 9 vector containing human Iduronate-2-sulfatase transgene |
|---|---|
| Trade Name | |
| Orphan Indication | Hunter Syndrome |
| USA Market Approval | USA |
| USA Designation Date | 2015-07-16 00:00:00 |
| Sponsor | Laboratorios del Dr. Esteve, S.A.;Av. Marie de Deu de Montserrat, 221;Barcelona |
