Synthetic double-stranded small interfering RNA (siRNA) oligonucleotide targeting delta-aminoevulinic acid synthase 1

Synthetic double-stranded small interfering RNA (siRNA) oligonucleotide targeting delta-aminoevulinic acid synthase 1
Trade Name
Orphan Indication Variegate porphyria
USA Market Approval USA
USA Designation Date 2016-08-29 00:00:00
Sponsor Alnylam Pharmaceuticals;300 Third Street;Cambridge, Massachusetts, 02142