Synthetic double-stranded siRNA oligonucleotide directed against delta-aminolevulinic acid synthase 1 mRNA covalently linked to a ligand containing three N-acetylgalactosamine residues

Synthetic double-stranded siRNA oligonucleotide directed against delta-aminolevulinic acid synthase 1 mRNA covalently linked to a ligand containing three N-acetylgalactosamine residues
Trade Name
Orphan Indication Variegate porphyria
EU Market Approval EU
EU Designation Date 2016-08-29 00:00:00
Sponsor Alnylam UK Limited