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Synthetic double-stranded siRNA oligonucleotide directed against delta-aminolevulinic acid synthase 1 mRNA covalently linked to a ligand containing three N-acetylgalactosamine residues |
|---|---|
| Trade Name | |
| Orphan Indication | Variegate porphyria |
| EU Market Approval | EU |
| EU Designation Date | 2016-08-29 00:00:00 |
| Sponsor | Alnylam UK Limited |
