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adeno-associated viral vector containing DNA encoding an RNAi targeting rhodopsin in combination with an adeno-associated viral vector containing DNA encoding a rhodopsin gene |
|---|---|
| Trade Name | Rhonova (Tm) |
| Orphan Indication | Retinitis pigmentosa |
| USA Market Approval | USA |
| USA Designation Date | 2012-12-13 00:00:00 |
| Sponsor | Spark Therapeutics Ireland Ltd.;Smurfit Institute of Genetics, Trinity College;Dublin 2 |
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