Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Country Product Indication Sponsor Date
Uridine 5′-triphosphate Primary ciliary dyskinesia Inspire Pharmaceuticals, Inc.;4222 Emperor Boulevard, Suite 470;Durham, North Carolina, 27703 June 26, 1996
Methylnaltrexone Chronic opioid-induced constipation unresponsive to conventional therapy Progenics Pharmaceuticals, Inc.;765 Old Saw Mill River Rd.;Tarrytown, New York, 10591 June 17, 1996
Selective inhibitor of polymorphonuclear leukocyte (PMN) elastase Therapeutic management of patients with lung disease attributable to cystic fibrosis DuPont Pharmaceuticals Company;Chestnut Run, Maple Run, Centre Rd.;Wilmington, Delaware, 19805 June 4, 1996
Collagenase clostridium histolyticum Advanced (involutional or residual stage) Dupuytren's disease Auxilium Pharmaceuticals, Inc.;40 Valley Stream Parkway;Malvern, Pennsylvania, 19335 May 23, 1996
Arcitumomab Diagnosis and localization of primary, residual, recurrent and metastatic medullary thyroid carcinoma Immunomedics, Inc.;300 American Road;Morris Plains, New Jersey, 07950 May 10, 1996
Etiocholanedione Prader-Willi syndrome SuperGen, Inc.;4140 Dublin Blvd., Suite 200;Dublin, California, 94568 May 7, 1996
Amphotericin B lipid complex Invasive coccidioidomycosis The Liposome Company, Inc.;One Research Way;Princeton, New Jersey, 08540 May 6, 1996
Amphotericin B lipid complex Invasive zygomycosis The Liposome Company, Inc.;One Research Way;Princeton, New Jersey, 08540 May 6, 1996
Liposomal prostaglandin E1 injection Acute respiratory distress syndrome Liposome Company, Inc.;One Research Way;Princeton, New Jersey, 08540 April 25, 1996
Idoxuridine Nonparenchymatous sarcomas NeoPharm, Inc.;225 East Deerpath, Suite 250;Lake Forest, Illinois, 60045 April 8, 1996
Lipid/DNA human cystic fibrosis gene Cystic fibrosis Genzyme Corporation;Metrowest Place, 15 Pleasant St. Connector;Framingham, Massachusetts, 01701 April 8, 1996
Somatropin (r-DNA) for injection Children with AIDS-associated failure-to-thrive including AIDS-associated wasting EMD Serono, Inc.;One Technology Place;Roackland, Massachusetts, 02370 March 26, 1996
Collagenase clostridium histolyticum Peyronie's disease Auxilium Pharmaceuticals, Inc.;640 Lee Road;Chesterbrook, Pennsylvania, 19087 March 12, 1996
Rifapentine Prophylactic treatment of Mycobacterium avium complex in patients with AIDS and a CD4+ count less than or equal to 75/mm3 Hoechst Marion Roussel, Inc.;P.O. Box 9627, Mail Station: H3-M2516;Kansas City, Missouri, 64134 March 12, 1996
N-[4-(trifluoromethyl)phenyl]-5-methylisoxazole-4-carboxamide Ovarian cancer Sugen, Inc.;230 East Grand Ave.;South San Francisco, California, 94080 March 12, 1996
Interferon beta-1a Patients with secondary progressive multiple sclerosis EMD Serono, Inc.;One Technology Place;Rockland, Massachusetts, 02370 March 11, 1996
Thalidomide HIV-associated wasting syndrome Celgene Corporation;7 Powder Horn Dr.;Warren March 11, 1996
Antihemophilic factor (recombinant) Hemophilia A Wyeth Pharmaceuticals, Inc.;P. O. Box 8299;Philadelphia, Pennsylvania, 19101 February 8, 1996
Testosterone Weight loss in AIDS patients with HIV-associated wasting Unimed Pharmaceuticals, Inc.;901 Sawyer Rd.;Marietta, Georgia, 30062 February 5, 1996
Dihydrotestosterone Weight loss in AIDS patients with HIV-associated wasting Besins Internaitonal, US Inc.;610 Herndon Parkway, Suite 750;Herndon, Virginia, 20170 February 5, 1996
Albendazole Neurocysticercosis due to Taenia solium as: 1) chemotherapy of parenchymal, subarachnoidal and racemose (cysts in spinal fluid) neurocysticercosis in symptomatic cases and 2) prophylaxis of epilepsy and other sequelae in asymptomatic neurocysticercosis Amedra Pharmaceuticals LLC;2 Walnut Grove Drive, Suite 190;Horsham, Pennsylvania, 19044 January 18, 1996
Albendazole Alveolar echinococcosis Amedra Pharmaceuticals LLC;2 Walnut Grove Drive, Suite 190;Horsham, Pennsylvania, 19044 January 17, 1996
Valine, isoleucine and leucine Hyperphenylalaninemia Leas Research Products;78 Fallon Drive;North Haven, Connecticut, 06473 January 5, 1996
Antihemophilic factor (human) Von Willebrand disease Grifols Biologicals Inc.;5555 Valley Boulevard;Los Angeles, California, 90032 January 5, 1996
Mecasermin Growth hormone insensitivity syndrome Ipsen Biopharmaceuticals, Inc.;106 Allen Road;Basking Ridge, New Jersey, 07920 December 12, 1995