Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Country Product Indication Sponsor Date
Nitric oxide Acute respiratory distress syndrome Mallinckrodt Hopspital Products;1425 U.S. 206;Bedminster Township, New Jersey, 07921 July 10, 1995
Ancestim For use in combination with filgrastim to decrease the number of phereses required to collect peripheral blood progenitor cells capable of providing rapid multi-lineage hematopoietic reconstitution following myelosuppressive or myeloablative therapy Amgen, Inc.;One Amgen Center Drive;Thousand Oaks, California, 91320 July 5, 1995
Encapsulated porcine islet preparation Type I diabetic patients who are already on immunosuppression VivoRx;2825 Santa Monica Blvd., 2nd Floor;Santa Monica, California, 90404 July 5, 1995
Trisodium citrate concentration For use in leukapheresis procedures Hemotec Medical Products, Inc.;Box 19255;Johnston, Rhode Island, 02919 June 15, 1995
Rifapentine Pulmonary tuberculosis Hoechst Marion Roussel;P.O. Box 9627, Mail Station: H3-M2516;Kansas City, Missouri, 64134 June 9, 1995
Rifapentine Mycobacterium avium complex in patients with AIDS Hoechst Marion Roussel , Inc.;P.O. Box 9627, Mail Station: H3-M2516;Kansas City, Missouri, 64134 June 9, 1995
Recombinant human insulin-like growth factor 1 Growth hormone deficiency Pharmacia & Upjohn;7000 Portage Road;Kalamazoo, Michigan, 49001 June 7, 1995
Ganciclovir intravitreal implant Cytomegalovirus retinitis Bausch & Lomb Surgical, Chiron Vision Products;9342 Jeronimo Road;Irvine, California, 92718 June 7, 1995
Recombinant human insulin-like growth factor 1 Growth hormone receptor deficiency Pharmacia & Upjohn;7000 Portage Road;Kalamazoo, Michigan, 49001 June 7, 1995
N-[4-(trifluoromethyl)phenyl] 5 methylisoxazole-4-carboxamide Glioma Sugen, Inc.;230 East Grand Ave.;South San Francisco, California, 94080 May 25, 1995
Nitisinone Tyrosinemia type 1 Swedish Orphan Biovitrum AB;890 Winter Street, Suite 115;Waltham, Massachusetts, 02451 May 16, 1995
Thalidomide Treatment and prevention of recurrent aphthous ulcers in severely, terminally immunocompromised patients Andrulis Research Corporation;11800 Baltimore Avenue, Suite 113;Beltsville, Maryland, 20705 May 15, 1995
Thalidomide Aphthous stomatitis Celgene Corporation;7 Powder Horn Dr.;Warren May 1, 1995
Clotrimazole Sickle cell anemia Brugnara, Carlo M.D.;The Children's Hospital, 300 Longwood Avenue, Bader 760;Boston, Massachusetts, 02115 April 24, 1995
Cystic fibrosis Tr gene therapy (recombinant adenovirus) Cystic fibrosis GenVec, Inc.;12111 Parklawn Drive;Rockville, Maryland, 20852 March 9, 1995
Facilitated DNA Plasmid Vaccine Cutaneous T-cell lymphoma Wyeth-Lederle Vaccines and Pediatrics;211 Bailey Rd.;West Henrietta, New York, 14586 March 8, 1995
Phenylalanine ammonia-lyase Hyperphenylalaninemia BioMarin Pharmaceutical;105 Digital Drive;Novato, California, 94949 March 8, 1995
Tyloxapol Cystic fibrosis Kennedy & Hoidal, M.D.'s;University of Utah Health Sciences Center, 50 North Medical Drive, Room 4R240;Salt Lake City, Utah, 84132 March 8, 1995
Hepatitis B immune globulin intravenous (human) Prophylaxis against hepatitis B virus reinfection in liver transplant patients Biotest Pharmaceuticals Corporation;5800 Park of Commerce Blvd., NW;Boca Raton, Florida, 33487 March 8, 1995
Somatropin (r-DNA) For use alone or in combination with glutamine in the treatment of short bowel syndrome EMD Serono, Inc.;One Technology Place;Roackland, Massachusetts, 02370 March 6, 1995
Sargramostim Acute myeloid leukemia Immunex Corporation;51 University Street;Seattle, Washington, 98101 March 6, 1995
Glutamine Short bowel syndrome Emmaus Medical, Inc.;20725 S. Western Avenue, Suite 136;Torrence, California, 90501 March 6, 1995
Recombinant human gelsolin Acute and chronic respiratory symptoms of bronchiectasis BioAgeis, Therapeutics, Inc.;6 East Cove Lane;Morristown, New Jersey, 07960 March 6, 1995
Adeno-associated viral-based vector cystic fibrosis gene therapy Cystic fibrosis Targeted Genetics Corporation;1100 Olive Way, Suite 100;Seattle, Washington, 98101 February 15, 1995
Glyceryl trioleate and glyceryl trierucate X-linked adrenoleukodystrophy Moser, Hugo W. M.D.;Johns Hopkins University, Kennedy Krieger Institute, 707 North Broadway;Baltimore, Maryland, 21205 February 14, 1995