DALLAS, Texas — Taysha Gene Therapies, Inc. (Nasdaq: TSHA) (Taysha or the Company), a clinical-stage biotechnology company focused on advancing adeno-associated virus (AAV)-based gene therapies for severe monogenic diseases of the central nervous system (CNS), today announced results from a new supplemental data analysis from Part A of the REVEAL...
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DALLAS – Taysha Gene Therapies, Inc. (Nasdaq: TSHA), a patient-centric, pivotal-stage gene therapy company focused on developing and commercializing AAV-based gene therapies for the treatment of monogenic diseases of the central nervous system (CNS) in both rare and large patient populations, today announced that it has been granted orphan drug...
DALLAS, Texas — Taysha Gene Therapies, Inc. (Nasdaq: TSHA) (Taysha or the Company), a clinical-stage biotechnology company focused on advancing adeno-associated virus (AAV)-based gene therapies for severe monogenic diseases of the central nervous system (CNS), today announced that it will present new preclinical in vitro data from a head-to-head evaluation...
A research team led by a University of Iowa investigator has generated DNA-like compounds that effectively inhibit the cells responsible for systemic lupus erythematosus — the most common and serious form of lupus. There currently is no cure for this chronic autoimmune condition that damages the skin, joints and internal...
SAN ANTONIO, Texas — The 50 families stretch from the Netherlands and the United Kingdom to the United States and China. Each family has a child who is paralyzed from a mutation in a single gene named Contactin-Associated Protein 1 (Cntnap1). The children are locked inside their bodies, unable to...
AyuVis Research Inc., a TechFW client, has been granted Orphan Drug Designation from the U.S. Food and Drug Administration (FDA) for its small molecule drug AVR-48 for the prevention of bronchopulmonary dysplasia or BPD. AVR-48 works to modulate the immune system by decreasing the inflammatory response to MV and oxygen...
BEERSE, BELGIUM, March 10, 2026 (GLOBE NEWSWIRE) — Johnson & Johnson today announced the submission of a Type II variation application to the European Medicines Agency (EMA) seeking approval for an indication extension of TECVAYLI®▼(teclistamab) as monotherapy for the treatment of adult patients with relapsed/refractory multiple myeloma (RRMM) who have received...
It’s not easy for Crystal Martinez to keep on top of her busy schedule. Along with her schoolwork as a student at Pocono Mountain West High School, she also has a hectic schedule of singing engagements extending through the summer, including one that will be before 100,000 people at the...
Hattiesburg, Miss. – A teenager in Mississippi is living with a disease so rare that less than 20 people worldwide have ever been diagnosed with it. Symptoms for 16-year-old Trey Garczynski started when he was 11 years old. “I was just walking around, but just a few minutes later, my...
HAMPTON, Conn. — A parent’s worst nightmare is that their child will suffer from a life-threatening disease with no cure on the horizon. But a family in Hampton said it’s putting all of its hopes into an experimental stem cell treatment and is traveling to Germany for the surgery. In...