Covina, California, USA — In a recent report titled “Rare Disease Market Report Explored in Latest Research by 2027,” published by Prophecy Market Insights, the market for rare diseases was estimated to be worth US$ 161.4 billion in 2020 and is expected to grow to US$ 547.5 billion by 2030,...
Latest News
HRA Pharma Rare Diseases and Celnova Pharma are partnering to meet a major unmet need for rare disease drugs in South America.
At the PDA Annual Meeting this week in New Orleans, attendees had the chance to hear from EveryLife Foundation executive director and leader of a number successful initiatives, Julia Jenkins, on the economic impact of rare disease in the U.S. and Kelly Baker, a member of the Young Adult Rare...
The new Rare Disease Policy 2021 is a positive step, but more needs to be done, experts and patients in the sector have asserted. “Implementation through multi-stakeholder planning and equity consideration and strengthening sensitization/ awareness efforts, new-borne screening tests in every hospital to ensure early detection and treatment, insurance coverage,...
Bethesda, Md. — HYFTOR® (sirolimus topical gel) 0.2%, indicated for the treatment of facial angiofibroma associated with tuberous sclerosis complex (TSC) in adults and pediatric patients 6 years of age and older, is now covered by Medicare in Texas, Florida, New York, and California, among other states. Nobelpharma, a pharmaceutical...
London, UK – Patients with rare diseases could benefit from a “revolution” in clinical trials that could see one-stop studies designed that provide robust results even with small numbers of participants. The CAPTIVATE node is part of the recently introduced UK Rare Disease Research Platform established as part of a...
Last month, Jessie Jackson’s friends and family sang her happy birthday a little early. Jessie doesn’t turn 30 until Dec. 12, but for the past five years on the anniversary of her diagnosis, her parents have hosted a fundraiser. They weren’t taking any chances. Jessie inherited a rare genetic condition called GM1...
Rare diseases are a serious public health concern in India, with an estimated burden of about 80 to 96 million cases reported annually. Moreover, 70-80% of rare diseases are of genetic nature and thus are asymptomatic. Here are their causes, signs, symptoms and treatment
February 25th was a busy day at the oval and the Recreation Complex. Many people showed up to give their support for the Canadian Organization for Rare Diseases (CORD). One of our own little citizens, 15-month-old Iris Mae McKechnie was diagnosed with infantile onset pompe disease and as a result...
Rare Diseases South Africa (RDSA) held its annual Denim Walk at Walter Sisulu Botanical Garden on March 4. Family, friends, survivors, and sufferers turned lush green lawns into a sea of white cotton and blue denim. South Africa has just short of four million suffering from rare genetic and congenital...