Rare diseases are not so rare. While a single rare disease may only affect a small proportion of the population, as many as 10% of Americans live with rare diseases, and most of those 30 million people have limited or no treatments and lack access to expert care. Now, Yale...
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NEW YORK – Research into treatment for the ultra-rare HNRNPH2 related disorder received a major boost from the MUNCH Project. The Yellow Brick Road Project (YBRP) supports individuals with the disorder and their families and raised 134 ETH tokens worth roughly $320,000 towards the first privately funded research project into treatment for this...
SHANGHAI – Shanghai Yingli Pharmaceuticals Ltd (Yingli Pharma), a clinical stage pharmaceutical company providing new therapies for cancer and metabolic diseases, announced today the topline data from a clinical trial sponsored by the company at the annual meeting of the European Hematology Association (EHA) being held June 9-17, 2021. The study...
Los Angeles, California – A new UCLA Health study found Kundalini yoga provided several benefits to cognition and memory for older women at risk of developing Alzheimer’s disease including restoring neural pathways, preventing brain matter decline and reversing aging and inflammation-associated biomarkers – improvements not seen in a group who...
SHANGHAI, China — YolTech Therapeutics announced that the first patient has been dosed with YOLT-101, the company’s in vivo genome editing candidate being developed as a single dose, potentially curative therapy for Familial Hypercholesterolemia(FH), marking the commencement of an Investigator-Initiated Trial (IIT). Familial Hypercholesterolemia (FH) is a genetic disorder that...
A young Galway dad has had his life turned upside down after a sneeze led to a horror injury giving him the back of a 90-year-old man. It was in July last year when 36-year-old Adrian Gordon sneezed and felt his back pop, leading to a horrific six months of...
After Kara Miller woke up with blurry vision she couldn’t blink away, her primary care doctor spotted something that would change her life. Kara, then 17, had a lesion on one of her optic nerves. Not only did the damaged nerve explain why she was seeing double, it was telltale...
Corbeil-Essonnes (near Paris), France – Yposkesi, a leading Contract Development and Manufacturing Organization (CDMO) specializing in cell and gene therapies, today announces the launch of project SKY, the construction of Yposkesi’s second commercial cell and gene therapy facility and new global resource for drug developers of biologics, also called ATMPs...
Cologne, Germany – Zanubrutinib, a second-generation Bruton tyrosine kinase (BTK) inhibitor, is approved for several therapeutic indications. The German Institute for Quality and Efficiency in Health Care (IQWiG) investigated whether the drug has an added benefit compared with the appropriate comparator therapy for adult patients with chronic lymphocytic leukaemia (CLL)...
DUARTE, California – The novel drug, zanzalintinib (XL092), showed promising cancer-fighting abilities in patients with advanced clear-cell renal cell carcinoma (ccRCC), according to initial results from the STELLAR-001 clinical trial. According to trial results, which were presented at the 2023 International Kidney Cancer Symposium, antitumor activity was observed in patients...