The Food and Drug Administration (FDA) is announcing a public Workshop entitled “Complex Issues in Developing Drug and Biological Products for Rare Diseases” The purpose of the workshop is to discuss complex issues in clinical trials for developing drug and biological products (“drugs”) for rare diseases, including endpoint development and...
Events
Pharmaceutical companies are facing the competitive atmosphere, increasing costs and necessity to keep up with the fast-changing environment. Clearly, these factors also influence the clinical trials that represent a key in advancing medical knowledge and further patient care. The 6th Annual Patient Recruitment and Retention in Pharma will lead you...
The aim of the 3rd LUNG CANCER Network “From the Bench to the Bedside” is to narrow the distance between the lab bench and the patient’s bed, between the clinical trials outcome and the routine practice, by bringing together basic scientists, clinical researchers and lung cancer specialists. Main Topics: End...
NextMed/MMVR explores data-enabled technology for clinical care and medical education. Primary topics are simulation, modeling, imaging, visualization, robotics, haptics, sensors, informatics, and data networking. “Medicine Meets Virtual Reality” was conceived in 1991 to explore the healthcare utilization of rapidly evolving computing and communications technologies. Physicians, educators, scientists, and engineers gathered...
PNH FAQ Webinar: Living Well Forum for Patients and Families During this webinar, Dr. David Araten, a specialist with many years of treating patients with Paroxysmal nocturnal hemoglobinuria (PNH), will answer questions that were pre-submitted and also take live questions about PNH. Dr. Araten will pull from his clinical background...
Webinar – MDS in Children: What Parents Need to Know Though myelodysplastic syndrome (MDS) occurs mainly in adults, it can occur in children. Pediatric MDS disease progression, prognosis, and outcomes are different for each child. How are these younger patients diagnosed and treated? During this webinar, Dr. Hofmann will explain...
World Rare Disease Day 2014 Planning Webinar: Ideas and Suggestions to Host Your Own World Rare Disease Day Event December 11, 2013 – 11:00 am PT (60 minutes) Register today! With World Rare Disease Day right around the corner (February 28th), this session will explore event ideas to create awareness...
The ASHG Annual Meeting is the largest human genetics meeting and exposition in the world. ASHG members and leading scientists from around the world are selected to present their research findings at invited, platform, and poster sessions. Abstracts of work submitted for presentation at the Annual Meeting will be published...
The goals of the International Osteogenesis Imperfecta conference involve continued stimulation of the rapid and exciting pace of OI research, specifically: 1) to bring together the basic and clinical international experts on OI for a full and frank exchange of the latest unpublished data, where clinicians and basic researchers can each...
The goals of the National Forum on Biomedical Innovation: Identifying Challenges and Prioritizing Needs in Medical Devices Research and Development is to bring together the leaders in the field of research, development and commercialization of medical devices to discuss the major issues that prevent full innovation in medical devices in...
Developing an Interdisciplinary Research Agenda for Genetics of Birth Defects Wednesday, January 22, 2014 Washington Dulles Airport Marriott, Sterling, VA The “white paper” summarizing the meeting proceedings and major conclusions will be published, shared via NIH and CDC websites, and distributed to participating stakeholders for further dissemination. The intent...
The XIII. International Congress on Neuromuscular Diseases is the regular meeting of the Research Group on Neuromuscular Diseases-World Federation of Neurology (RGNMD-WFN) hosted all around the world as a every 4-year event from now more than 50 years. It is firmly established by the global neuromuscular community as the most...
International GSD Conference 2013 28-30 November 2013, Heidelberg, Germany For the first time, an international conference will bring together liver and muscle types of glycogen storage disease (GSD). World experts will discuss the state of research and therapies for the muscle and liver types in parallel sessions. The exchange of...
The goal of “BDA workshop Improving oncology drug development for children and adolescents” is to state where we are, to identify how the strategy for pediatric oncology drug development should be further defined and to propose solutions that may improve the implementation of the regulation in order to better meet...
2014 Moebius Syndrome Foundation Conference will offer an incredible opportunity for people with Moebius syndrome to meet others with the same condition, to connect with old friends and make new, lifelong friends. There will be presentations, workshops and support sessions as well as consult and research opportunities. Special sessions will...
CurePSP (Foundation for PSP | CBD and Related Brain Diseases) conducts an annual Research Symposium to facilitate dissemination of advances in the fields of PSP, CBD and related brain diseases. This annual symposium highlights research by CurePSP grantees and will be open to all researchers interested in clinical and basic...
In March of 2014, the Meso Foundation’s Symposium will be back in the Washington, DC metro area. The conference will be held at the Hilton Alexandria Mark Center (located at 5000 Seminary Road, Alexandria, VA) from Wednesday March 5th through Friday March 7th. On Wednesday, we will travel to Capitol...
The 7th Annual Fibromuscular Dysplasia Society of America Conference will be held in Cleveland, OH, USA. Hear the most recent findings from the Fibromuscular Dysplasia Patient Registry and other FMD related topics. Speakers will be announced at a later date. After all speakers have finished questions will be taken from...
“Betting on Ataxia Research” The National Ataxia Foundation 57 th Annual Membership Meeting 2014 The National Ataxia Foundation (NAF) Board of Directors and the National Ataxia Foundation Western Region Support Groups invite you to attend the 57th “Betting on Ataxia Research” Annual Membership Meeting (AMM). Please join us at Bally’s...
Please join us at the Penn Museum for the “Center for Orphan Disease Research and Therapy – First Annual Fall Retreat on Rare Diseases”. The day will start at 8:30 with a continental breakfast followed by an overview of the center and by presentations on opportunities in rare disease research...