The World Orphan Drug Congress Asia 2014 is Asia’s largest orphan drug industry event. This event is committed to fostering partnerships and relationships between industry, governments, payers, investors and patients. It is about expediting orphan drug development and articulating its value, from discovery to clinical development, to licensure, to manufacturing,...
Events
World Orphan Drug Congress USA is where industry, government, payers and patient groups come together to uncover the best strategies and technologies to improve orphan drug development, licensure, manufacture, product launch, supply and reimbursement. By uniting key stakeholders and decision makers, World Orphan Drug Congress USA provides an unrivalled platform...
International Consensus Conference to Develop Improvement Criteria for Juvenile Dermatomyositis and Adult Dermatomyositis and Polymyositis: Workshop to Define Minimal Clinical Improvement and Major Clinical Response Anticipated goals and use of results: We anticipate developing composite endpoints for future clinical trials that will be fully validated, endorsed by the ACR...
Lysosomal Disease Network – 10th Annual WORLD Symposium™ 2014 Overview: The goal of the Lysosomal Disease Network™ (LDN) is to provide an interdisciplinary forum to explore and discuss specific areas of interest, research and clinical applicability related to lysosomal diseases. This symposium is designed to help researchers and clinicians to...
Join the Commercialisation of Orphan & Rare Disease Drugs 2014 conference taking place 20-21 March 2014 in central London. With a strategic, high level focus on navigating the niche drug market, this forum provides a unique opportunity to meet, network and hear from acknowledged industry experts. Discover untapped revenue streams...
The 5th European Symposium on Rare Anaemias and 1st Italian Thalassaemia Meeting for Patients and Health Professionals is a unique chance to access up-to-date knowledge and work in a transversal environment. This event provides an overview on prevention, diagnosis and clinical management of thalassaemia and other haemoglobinopathies. Assistants will debate...
The European Conference on Rare Diseases & Orphan Products (ECRD) is the unique forum across all rare diseases, across all European countries, bringing together all stakeholders: patients’ representatives, academics, health care professionals, industry, regulators and policy makers. ECRD provides the state of the art of the rare disease environment, monitoring...
The Presidential Commission for the Study of Bioethical Issues recently released a report entitled Privacy and Progress in Whole Genome Sequencing. In short, it concludes that “to realize the enormous promise that whole genome sequencing holds for advancing clinical care and the greater public good, individual interests in privacy must...
We are celebrating our 21st year of providing information about the disorder to families all over the world! Joubert Syndrome and its related disorders are rare genetic disorders characterized by decreased muscle tone, difficulties with coordination, abnormal eye movements, abnormal breathing pattern and cognitive impairment. Joubert Syndrome is one of...
Welcome to the American Neurological Association’s 2013 Annual Meeting site! With the simple buttons below and to the right, you can not only register to attend the meeting, but you can also find a wealth of information about ANA2013 scientific programs, professional development courses, Interactive Lunch Workshops and more! This...
CAMBRIDGE, MA – Sarepta Therapeutics, Inc., a developer of innovative RNA-based therapeutics, will host a webcast and conference call for the Duchenne muscular dystrophy (DMD) community on Thursday, October 17, 2013, beginning at 12:00 p.m., Eastern Time (9:00 a.m., Pacific Time). Chris Garabedian, president and chief executive officer, and Edward...
We invite you to the attend the Novel Immunotherapeutics Summit, which will take place on Jaunary 29 – 31, 2014 in San Diego, CA. The summit will bring together our usual balance of industry and academia, so that delegates have the unique opportunity to network with colleagues from different sectors and gain fresh...
GTC is proud to announce its 2nd Immunogenicity and Immunotoxicity Conference, one of four parallel tracks to the Novel Immunotherapeutics Summit 2014 on January 29 – 31, 2014 in San Diego, CA. The conference will cover important progress made in the areas of therapeutic protein immunogenicity and immunotoxicity evaluation such as protein aggregation, clinical...
6th Ocular Diseases Drug Discovery Conference is taking place on February 20-21, 2014 in San Diego, CA. The conference continues to offer presentations on novel and innovative therapeutics in ocular drug development and discovery. This forum allows for excellent networking, the exchange of ideas, and sharing of challenges; all with a...
The 7th Oncology Biomarkers Conference is one of three conferences part of the Biomarker Summit 2014 to be held on March 19-21, 2014 in San Diego, CA. This conference brings together experts in industry, academia and government to discuss the latest developments in the oncology biomarker research arena. Hot topics...
The 3rd Neurological Biomarkers Conference is one of three conferences part of the Biomarker Summit 2014 to be held on March 19-21, 2014 in San Diego, CA. This conference focuses on the development of CNS biomarkers for drugs and diagnostics from CSF and imaging approaches. Scientific data, updates and case...
The 3rd Inflammatory & Immunological Biomarkers Conference is one of three conferences part of the Biomarker Summit 2014 to be held on March 19-21, 2014 in San Diego, CA. As the name suggests, this conference will cover both inflammatory and immunological biomarkers in a wide variety of disease areas including...
We invite you to attend the Stem Cell Summit 2014 taking place on April 23-25, 2014 inBoston, MA. This summit includes two parallel conferences which include joint sessions. GTC’s Stem Cell Summit 2014 provides cutting-edge information on developments in all areas of stem cell research including the biology, medicine, applications, regulations, and the business of Stem...
We welcome you to GTC’s Stem Cell Research & Regenerative Medicine Conference which is also part of the Stem Cell Summit 2014 to be held on April 24-25, 2014 in Boston, MA. This conference presents information regarding cutting-edge developments in all areas of stem cell research including the biology, medicine, applications and regulations of stem cells. Recent...
We welcome you to GTC’s Stem Cell Commercialization & Partnering Conference, which is also part of the Stem Cell Summit 2014 to be held on April 24-25, 2014 in Boston, MA. This forum presents information regarding cutting-edge developments in all areas of stem cell research including the biology, medicine, applications, regulations and business of stem cells....