Safety and Efficacy Evaluation of β-globin Restored Autologous Hematopoietic Stem Cells in β-thalassemia Major Patients

Beta-thalassemia

NAC Effect on Iron Overload and Blood Transfusion in β-thalassemia Major A Study of Immune Suppression Treatment for People With Sickle Cell Disease or β-Thalassemia Who Are Going to Receive an Allogeneic Hematopoietic Cell Transplantation (HCT) A Trial Testing SP-420 in Subjects With Transfusion-dependent β-thalassemia Safety and Efficacy Evaluation of BRL-101 in Subjects With Transfusion-Dependent β-Thalassemia A Study to Evaluate Luspatercept (ACE-536) in Chinese Participants Who Require Regular Red Blood Cell Transfusions Due to Beta (β)-Thalassemia. Atrial Fibrillation in Beta-Thalassemia The Safety and Efficiency of Luspatercept in Chinese Adults With Transfusion Dependent β-thalassemia: a Real-world Study Assessment of Cognitive Function, Fatigue and Health Related Quality of Life in Children With Beta Thalassemia Safety and Efficacy Evaluation of γ-globin Reactivated Autologous Hematopoietic Stem Cells EDIT-301 for Autologous Hematopoietic Stem Cell Transplant (HSCT) in Participants With Transfusion-Dependent Beta Thalassemia (TDT) The Prevelence of IVS 1-6 (T-C) [HBB:c.92 +6 T-C] Gene Mutation in Suspected Cases of β Thalassemia in Assiut University Hospitals Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Transfusion-Dependent β-Thalassemia (TDT) Study on the Effect of Different Risk Factors on the Growth Parameters of Thalassemic Patients in Assiut (AUCH) The Prevelence of HBB c.93-21 G-A in β Thalassemia Patients Study to Evaluate Additional Risk Minimisation Measures (aRMMs) for REBLOZYL Among Healthcare Professionals (HCPs) Thrombin Generation in Beta-thalassemia Major Iron Status in BTM With Blood Transfusion Efficacy and Safety Study of Multiple Doses of VIT-2763 in Adults With Transfusion-dependent Beta-thalassemia Genetic Variants Affecting the Clinical Severity of Beta Thalassemia Association of Hb F Level With Clinical Severity of Beta Thalassemia Safety and Efficacy Evaluation of β-globin Restored Autologous Hematopoietic Stem Cells in β-thalassemia Major Patients The Role of OCTA in Patients Affected by Beta Thalassemia