Adeno-associated viral vector serotype 8 encoding engineered rhodopsin DNA-binding repressor and human rhodopsin expression cassettes | |
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Trade Name | |
Orphan Indication | Retinitis pigmentosa |
EU Market Approval | EU |
EU Designation Date | 2016-12-12 00:00:00 |
Sponsor | Fondazione Telethon |
Related Access Program