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Synthetic double-stranded small interfering RNA (siRNA) oligonucleotide targeting delta-aminoevulinic acid synthase 1 |
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| Trade Name | |
| Orphan Indication | Variegate porphyria |
| USA Market Approval | USA |
| USA Designation Date | 2016-08-29 00:00:00 |
| Sponsor | Alnylam Pharmaceuticals;300 Third Street;Cambridge, Massachusetts, 02142 |
