Adeno-associated virus serotype 2/6 (rAAV2/6) vectors encoding zinc finger nucleases (ZFNs) and the human iduronate 2-sulfatase (hIDS) gene | |
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Trade Name | |
Orphan Indication | Hunter Syndrome |
USA Market Approval | USA |
USA Designation Date | 2017-02-27 00:00:00 |
Sponsor | Sangamo Therapeutics, Inc.;Point Richmond Tech Center, 501 Canal Boulevard;Richmond, California, 94804 |