Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Country Product Indication Sponsor Date
Ascorbic acid Scurvy McGuff Pharmaceuticals Inc.;2921 W. McArthur Blvd., Suite 141;Santa Ana, California, 92704 August 31, 2007
Pafuramidine maleate African trypanosomiasis Immtech Pharmaceuticals, Inc.;150 Fairway Drive;Vernon Hills, Illinois, 60061 August 31, 2007
4-Amino-1-[5-O-[(2R, 4S)-2-oxido-4-(4-pyridinyl)-1, 3, 2-dioxaphosphorinan-2-yl]-b-D-arabinofuranosyl]-2(1H)-pyrimidinone Hepatocellular Carcinoma Ligand Pharmaceuticals, Inc.;11085 N. Torrey Pines Road, Suite 300;LaJolla, California, 92037 August 22, 2007
Bendamustine hydrochloride Chronic lymphocytic leukemia Cephalon, Inc.;41 Moores Road;Frazer, Pennsylvania, 19355 August 17, 2007
Betulinic acid Metastatic Melanoma Advanced Life Sciences, Inc. (ALS);1440 Davey Road;Woodridge, Illinois, 60517 August 9, 2007
Talactoferrin alfa Non-small cell lung cancer Agennix, Inc.;8 Greenway Plaza, Suite 910;Houston, Texas, 77046 August 8, 2007
N-(2-amino-phenyl)-4-[(4-pyridin-3-yl-pyrimidin-2-ylamino)-methyl] benzamide dihydrobromide Hodgkin’s disease Mirati Therapeutics, Inc.;9363 Towne Centre Drive, Suite 200;San Diego, California, 92121 August 8, 2007
Recombinant human soluble Fc-gamma receptor IIb Idiopathic thrombocytopenic purpura Baxalta Innovations GmbH August 2, 2007
Sodium ascorbate and menadione sodium bisulfite Transitional cell carcinoma IC-MedTech Corporation;9902 Indian Creek Lane;San Diego, California, 92021 July 31, 2007
Recombinant P-selectin glycoprotein ligand-immunoglobulin Ig Prevention of ischemia reperfusion injury in all solid organ transplants Y's Therapeutics, Inc.;1539 Granger Way;Redwood City, California, 94061 July 26, 2007
Intravenous immune globulin Metastatic Melanoma GammaCan Ltd.;39 Jerusalem Street; July 26, 2007
(R)-2-methyl-6-nitro-2-{4-[4-(4-trifluoromethoxyphenoxy)piperidin-1-yl]phenoxymethyl}-2,3-dihydroimidazo[2,1-b]oxazole Pulmonary tuberculosis Otsuka Pharmaceutical Company, Ltd;2440 Research Blvd;Rockville, Maryland, 20850 July 12, 2007
(3S)-3-(4-trifluoromethoxybenzyloxy)-6-nitro-2H-3,4-dihydroimidazo[2,1-b]oxazine Tuberculosis Global Alliance for TB Drug Development;40 Wall Street, 24th Floor;New York, New York, 10005 July 5, 2007
Cordycepin Acute lymphoblastic leukemia OncoVista, Inc.;14785 Omicron Drive;San Antonio, Texas, 78245 July 5, 2007
5,7-dihydroxy-3-(4-hydroxyphenyl)-chromen-4-one Acute Radiation Syndrome Acute radiation syndrome Humanetics Corporation;1550 Utica Avenue South, Suite 770;Eden Prairie, Minnesota, 55416 June 18, 2007
Duvoglustat hydrochloride Pompe disease Amicus Therapeutics, Inc;1 Cedarbrook Drive;Cranbury, New Jersey, 08512 June 18, 2007
Cetuximab Pancreatic Cancer ImClone Systems Incorporated;33 ImClone Drive;Branchburg, New Jersey, 08876 June 15, 2007
5(S)-(2′-hydroxy ethoxy)-20(S)-Camptothecin Pediatric osteosarcoma Dr. Reddy's Laboratories, Inc.;200 Somerset Corporate Blvd, Building II, 7th Floor;Bridgewater, New Jersey, 08807 June 15, 2007
5(S)-(2′-hydroxy ethoxy)-20(S)- camptothecin Ohtahara syndrome Dr Reddy's Laboratories (UK) Limited June 8, 2007
Autologous cultured endothelial cells on a donor human corneal disk Fuch's dystrophy, pseudophakic bullous keratopathy, and bullous keratopathy Cellular Bioengineering, Inc.;1946 Young Street;Honolulu, Hawaii, 96826 June 1, 2007
Axitinib Pancreatic Cancer Pfizer, Inc.;10646 Science Center Drive;San Diego, California, 92121 May 31, 2007
Plevitrexed Stomach Cancer BTG International Ltd;10 Fleet Place, London EC4M 7SB; May 29, 2007
N-[4-(3-amino1H-indazol-4-yl)phenyl]-N1-(2-fluoro-5-methylphenyl)urea Hepatocellular Carcinoma AbbVie, Inc.;1 N Waukegan Road, AP34/RA72;North Chicago, Illinois, 60064 May 23, 2007
Adeno-associated viral vector expressing human retinoschisin-1 gene X-linked Juvenile Retinoschisis Applied Genetic Technologies Corporation;11801 Research Drive;Alachua, Florida, 32615 May 21, 2007
Adeno-associated vector expressing the human lipoprotein lipase protein Lipoprotein lipase deficiency uniQure B.V.;Meibergdreef 61, 1100 DA;Amsterdam May 21, 2007