Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Country Product Indication Sponsor Date
Tissue repair cells obtained from autologous bone marrow expanded ex vivo with a cell production system Dilated cardiomyopathy Vericel Corporation.;Domino's Farms, Lobby L, 24 Frank Lloyd Wright Drive;Ann Arbor, Michigan, 48105 January 25, 2007
Microvesiculated modified glycosylated tissue factor Non-life threatening, mild to severe bleeding episodes due to cutaneous injuries or dental procedures in hemophiliac patients Thrombotargets Corp.;2530 Meridian Parkway, Suite 3023;Durham, North Carolina, 27713 January 25, 2007
Ixmyelocel-T Dilated cardiomyopathy Vericel Corporation.;Domino's Farms, Lobby L, 24 Frank Lloyd Wright Drive;Ann Arbor, Michigan, 48105 January 25, 2007
Droxidopa Orthostatic Hypotension Lundbeck LLC;Four Parkway North;Deerfield, Illinois, 60015 January 17, 2007
Sodium nitrite Prevention of vasospasm associated with subarachnoid hemorrhage Hope Pharmaceuticals;16416 N. 92nd Street;Scottsdale, Arizona, 85260 January 17, 2007
Dihydroartemisinin and piperaquine Malaria Leadiant Biosciences, Inc.;9841 Washingtonian Blvd., Suite 500;Gaithersburg, Maryland, 20878 January 8, 2007
Defibrotide For the prevention of hepatic veno-occlusive disease Jazz Pharmaceuticals, Inc.;3180 Porter Drive;Palo Alto, California, 94304 January 8, 2007
Cyclosporine A implant For the prevention of acute rejection in cornea transplant patients Lux Biosciences, Inc.;Harborside Financial Center, Plaza 10, 14th Floor;Jersey City, New Jersey, 07302 January 8, 2007
Liposomal doxorubicin hydrochloride Soft tissue sarcomas GP-Pharm SA;Pol. Ind. Els Vinyets els Fogars n 2,, Quinti de Mediona;Barcelona December 27, 2006
Liposomal ciprofloxacin for inhalation Bronchiectasis Aradigm Corporation;3929 Point Eden Way;Hayward, California, 94545 December 27, 2006
Tecovirimat Smallpox SIGA Technologies, Inc.;4575 SW Research Way, Suite 230;Corvallis, Oregon, 97333 December 27, 2006
Epstein Barr Virus specific cytotoxic T lymphocytes Prevention and treatment of EBV-post transplant lymphoproliferative disease after hematopoietic stem cell transplant or solid organ transplant Center for Cell and Gene Therapy;Feigin Center, Suite 1120;Houston, Texas, 77030 December 27, 2006
N-[3-(4′,5′-bipyrimidin-2-ylamino)-4-methylphenyl]-4-{[(3S)-3-(dimethylamino)pyrrolidin-1-yl]methyl}-3-(trifluoromethyl)benzamide Philadelphia chromosome-positive chronic myelogenous leukemia CytRx Corporation;3030 Bunker Hill Street, Suite 101;San Diego, California, 92109 December 27, 2006
Rose Bengal Disodium Metastatic Melanoma Provectus Pharmaceuticals, Inc.;7327 Oak Ridge Highway;Knoxville, Tennessee, 37931 December 21, 2006
Amonafide L-malate Acute myeloid leukemia Xanthus Pharmaceuticals, Inc.;An Antisoma Group Company, 300 Technology Square;Cambridge, Massachusetts, 02139 December 20, 2006
Cyclo {{(E,Z)-(2S,3R,4R)-3-hydroxy-4-methyl-2-(methylamino)nona-6,8-dienoyl}-L-2-aminobytyrl-N-methyl-glycyl-N-methyl-L-leucyl-L-valyl-N-methyl-L-leucyl-L-alanyl-D-alanyl-N-methyl-L-leucyl-N-methyl-L-leucyl-N-methyl-L-valyl} Treatment and chronic control of non-infectious posterior, intermediate and pan-uveitis Lux Biosciences, Inc.;Hoarborside Financial Center, Plaza 10, 14th Floor;Jersey City, New Jersey, 07302 December 20, 2006
Human cytomegalovirus immunoglobulin Prevention of congenital cytomegalovirus (CMV) infection following primary CMV infection in pregnant women Biotest Pharmaceuticals Corporation's (BPC);901 Yamato Road, Suite 101;Boca Raton, Florida, 33431 December 20, 2006
Budesonide Patients with eosinophilic esophagitis Meritage Pharma, Inc.;12555 High Bluff Drive, Suite 385;San Diego, CA, 92130 December 20, 2006
Amyl nitrite, sodium nitrite, sodium thiosulfate Cyanide poisoning Akorn, Inc.;2500 Millbrook Drive;Buffalo Grove, Illinois, 60089 December 18, 2006
Sodium thiosulfate and sodium nitrite Cyanide poisoning Akorn, Inc.;2500 Millbrook Drive;Buffalo Grove, Illinois, 60089 December 18, 2006
Iobenguane I 123 For the diagnosis of pheochromocytomas GE Healthcare, Inc.;101 Carnegie Center;Princeton, New Jersey, 08540 December 1, 2006
Iobenguane I 123 For the diagnosis of neuroblastomas GE Healthcare, Inc.;101 Carnegie Center;Princeton, New Jersey, 08540 December 1, 2006
Obatoclax mesylate Myelofibrosis Gemin X Pharmaceuticals US, Inc.;400 Chesterfield Pkwy., Suite 100;Malvern, Pennsylvania, 19355 December 1, 2006
Fenobam hydrochloride Fragile X syndrome Neuropharm, Ltd.;87 Church Street, Crowthorne, Berkshire; November 20, 2006
Varicella Zoster Immune Globulin (Human) Passive immunization for the treatment of exposed, susceptible individuals who are at risk of complications from varicella Cangene bioPharma, Inc.;155 Innovation Drive, Winnipeg;Manitoba R3T5Y3 November 7, 2006