autologous CD34+ hematopoietic stem cells tranduced with lentiviral vector Lenti-D encoding the human ABCD1 cDNA

autologous CD34+ hematopoietic stem cells tranduced with lentiviral vector Lenti-D encoding the human ABCD1 cDNA
Trade Name
Orphan Indication Andrenoleukodystrophy
USA Market Approval USA
USA Designation Date 2012-04-19 00:00:00
Sponsor bluebird bio, Inc.;60 Binney Street;Cambridge, Massachusetts, 02142