autologous CD34+ hematopoietic stem cells tranduced with lentiviral vector Lenti-D encoding the human ABCD1 cDNA | |
---|---|
Trade Name | |
Orphan Indication | Andrenoleukodystrophy |
USA Market Approval | USA |
USA Designation Date | 2012-04-19 00:00:00 |
Sponsor | bluebird bio, Inc.;60 Binney Street;Cambridge, Massachusetts, 02142 |