Exon 53 specific antisense morpholino oligonucleotide.

Exon 53 specific antisense morpholino oligonucleotide.
Trade Name
Orphan Indication Duchenne muscular dystrophy
USA Market Approval USA
USA Designation Date 2017-01-12 00:00:00
Sponsor NS Pharma, Inc.;140 East Ridgewood Avenue, Suite 280S;Paramus, New Jersey, 07652