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Non-replicating recombinant adeno-associated viral vector expressing the human acid alpha-glucosidase gene |
|---|---|
| Trade Name | |
| Orphan Indication | Pompe disease |
| USA Market Approval | USA |
| USA Designation Date | 2017-01-11 00:00:00 |
| Sponsor | Duke University Medical Center;Box 103856;Durham, North Carolina, 27710 |
