recombinant human acid a-glucosidase co-administered with N-butyl-deoxynojirimycin (reconbinant human acid a-glucosidase/miglustat)

recombinant human acid a-glucosidase co-administered with N-butyl-deoxynojirimycin (reconbinant human acid a-glucosidase/miglustat)
Trade Name
Orphan Indication Pompe disease
USA Market Approval USA
USA Designation Date 2017-09-13 00:00:00
Sponsor Amicus Therapeutics, Inc.;1 Cedarbrook Drive;Cranbury Township, New Jersey, 08512