recombinant adeno-associated virus serotype 8 vector encoding human glucose-6-phosphatase-alpha (G6Pase or G6PC)

recombinant adeno-associated virus serotype 8 vector encoding human glucose-6-phosphatase-alpha (G6Pase or G6PC)
Trade Name
Orphan Indication Von Gierke disease
USA Market Approval USA
USA Designation Date 2016-09-28 00:00:00
Sponsor Dimension Therapeutics;840 Memorial Drive;Cambridge, Massachusetts, 02139