|
recombinant adeno-associated virus serotype 8 vector encoding human glucose-6-phosphatase-alpha (G6Pase or G6PC) |
|---|---|
| Trade Name | |
| Orphan Indication | Von Gierke disease |
| USA Market Approval | USA |
| USA Designation Date | 2016-09-28 00:00:00 |
| Sponsor | Dimension Therapeutics;840 Memorial Drive;Cambridge, Massachusetts, 02139 |
