Adeno-Associated Viral Vector Expressing Low-Density Lipoprotein Receptor

Adeno-Associated Viral Vector Expressing Low-Density Lipoprotein Receptor
Trade Name
Orphan Indication Homozygous Familial Hypercholesterolemia
USA Market Approval USA
USA Designation Date 2012-01-31 00:00:00
Sponsor ReGenX Biosciences LLC;750 17th Street, NW, Suite 1100;Washington, District of Columbia, 20006